Showing results (211-220 of 223) with videos related to

Sort By:
Pageof 23
The Lancet. Neurology|February 21, 2023
Antisense oligonucleotide targeting DMPK in patients with myotonic dystrophy type 1: a multicentre, randomised, dose-escalation, placebo-controlled, phase 1/2a trialCharles A Thornton, Richard Thomas Moxley, Katy Eichinger, et al.
Annals of Clinical and Translational Neurology|April 16, 2025
Clinical Trial Readiness in Limb Girdle Muscular Dystrophy R1 (LGMDR1): A GRASP Consortium StudyStephanie M Hunn, Lindsay N Alfano, Aileen Jones, et al.
Clinical Cancer Research : an Official Journal of the American Association for Cancer Research|September 13, 2023
Osteosarcoma PDX-Derived Cell Line Models for Preclinical Drug Evaluation Demonstrate Metastasis Inhibition by Dinaciclib through a Genome-Targeted ApproachCourtney R Schott, Amanda L Koehne, Leanne C Sayles, et al.
Journal of Neuromuscular Diseases|February 6, 2026
A randomized, double-blind, placebo-controlled study of losmapimod in patients with facioscapulohumeral muscular dystrophy: Results of the REACH studyNicol C Voermans, Jeffrey M Statland, Lawrence J Hayward, et al.
Journal of Clinical Psychopharmacology|April 17, 2023
Escaping the Long Shadow Cast by Agranulocytosis: Reflections on Clozapine Pharmacovigilance Focused on the United KingdomJose de Leon, Manuel Arrojo-Romero, Hélène Verdoux, et al.
Biorxiv : the Preprint Server for Biology|January 30, 2023
Development and characterization of new patient-derived xenograft (PDX) models of osteosarcoma with distinct metastatic capacitiesCourtney R Schott, Amanda L Koehne, Leanne C Sayles, et al.
Annals of Clinical and Translational Neurology|December 15, 2024
Prospective observational study of FKRP-related limb-girdle muscular dystrophy R9: A GRASP consortium studyLindsay N Alfano, Meredith K James, Kristine Grosfjeld Petersen, et al.
Neuromuscular Disorders : NMD|April 10, 2026
Natural history of limb girdle muscular dystrophy R1 (LGMDR1): a GRASP consortium studyStephanie M Hunn, Andrew R Findlay, Lindsay N Alfano, et al.
The Lancet. Neurology|April 17, 2024
Safety and efficacy of losmapimod in facioscapulohumeral muscular dystrophy (ReDUX4): a randomised, double-blind, placebo-controlled phase 2b trialRabi Tawil, Kathryn R Wagner, Johanna I Hamel, et al.
Journal of Clinical Psychopharmacology|April 8, 2025
Letter to the FDA Proposing Major Changes in the US Clozapine Package Insert Supported by Clozapine Experts Worldwide. Part II: A Review of Fatal Outcomes in US Pharmacovigilance Data and Proposed ChangesJose de Leon, Ross J Baldessarini, Richard Balon, et al.
Pageof 23