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Human Mutation
|
November 7, 2019
Netrin-G2 dysfunction causes a Rett-like phenotype with areflexia
Gali Heimer, Geeske M van Woerden, Ortal Barel, et al.
Autophagy
|
November 21, 2020
A tecpr2 knockout mouse exhibits age-dependent neuroaxonal dystrophy associated with autophagosome accumulation
Bat-Chen Tamim-Yecheskel, Milana Fraiberg, Kamilya Kokabi, et al.
Molecular Therapy. Nucleic Acids
|
February 3, 2025
Personalized allele-specific antisense oligonucleotides for GNAO1-neurodevelopmental disorder
Inna Shomer, Nofar Mor, Shaul Raviv, et al.
Nature Metabolism
|
August 31, 2023
A defect in mitochondrial fatty acid synthesis impairs iron metabolism and causes elevated ceramide levels
Debdeep Dutta, Oguz Kanca, Seul Kee Byeon, et al.
International Journal of Molecular Sciences
|
July 12, 2025
A Novel Pathogenic Variant Identified in HIKESHI-Related Hypomyelinating Leukodystrophy Disrupts Heat Shock Response in iPSCs
Mahmood Ali Saleh, Maria Boichuck, Aner Ottolenghi, et al.
European Journal of Paediatric Neurology : EJPN : Official Journal of the European Paediatric Neurology Society
|
November 7, 2015
TECPR2 mutations cause a new subtype of familial dysautonomia like hereditary sensory autonomic neuropathy with intellectual disability
Gali Heimer, Danit Oz-Levi, Eran Eyal, et al.
European Journal of Human Genetics : EJHG
|
August 1, 2025
Biallelic MED29 variants cause pontocerebellar hypoplasia with cataracts
Leo Arkush, Geeske M van Woerden, Limor Ziv, et al.
Orphanet Journal of Rare Diseases
|
March 19, 2025
Clinical profiling and medical management of Israeli individuals with Phelan McDermid syndrome
Odelia Chorin, Lior Greenbaum, Shelly Lev-Hochberg, et al.
American Journal of Human Genetics
|
February 1, 2020
Bi-allelic Variants in RALGAPA1 Cause Profound Neurodevelopmental Disability, Muscular Hypotonia, Infantile Spasms, and Feeding Abnormalities
Matias Wagner, Yuliya Skorobogatko, Ben Pode-Shakked, et al.
Molecular Genetics and Metabolism
|
August 26, 2019
Cerebral and portal vein thrombosis, macrocephaly and atypical absence seizures in Glycosylphosphatidyl inositol deficiency due to a PIGM promoter mutation
Ben Pode-Shakked, Gali Heimer, Thierry Vilboux, et al.
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of 6
Search research articles
Search
Showing results (31-40 of 55) with videos related to
Sort By:
Page
of 6
Human Mutation
|
November 7, 2019
Netrin-G2 dysfunction causes a Rett-like phenotype with areflexia
Gali Heimer, Geeske M van Woerden, Ortal Barel, et al.
Autophagy
|
November 21, 2020
A tecpr2 knockout mouse exhibits age-dependent neuroaxonal dystrophy associated with autophagosome accumulation
Bat-Chen Tamim-Yecheskel, Milana Fraiberg, Kamilya Kokabi, et al.
Molecular Therapy. Nucleic Acids
|
February 3, 2025
Personalized allele-specific antisense oligonucleotides for GNAO1-neurodevelopmental disorder
Inna Shomer, Nofar Mor, Shaul Raviv, et al.
Nature Metabolism
|
August 31, 2023
A defect in mitochondrial fatty acid synthesis impairs iron metabolism and causes elevated ceramide levels
Debdeep Dutta, Oguz Kanca, Seul Kee Byeon, et al.
International Journal of Molecular Sciences
|
July 12, 2025
A Novel Pathogenic Variant Identified in HIKESHI-Related Hypomyelinating Leukodystrophy Disrupts Heat Shock Response in iPSCs
Mahmood Ali Saleh, Maria Boichuck, Aner Ottolenghi, et al.
European Journal of Paediatric Neurology : EJPN : Official Journal of the European Paediatric Neurology Society
|
November 7, 2015
TECPR2 mutations cause a new subtype of familial dysautonomia like hereditary sensory autonomic neuropathy with intellectual disability
Gali Heimer, Danit Oz-Levi, Eran Eyal, et al.
European Journal of Human Genetics : EJHG
|
August 1, 2025
Biallelic MED29 variants cause pontocerebellar hypoplasia with cataracts
Leo Arkush, Geeske M van Woerden, Limor Ziv, et al.
Orphanet Journal of Rare Diseases
|
March 19, 2025
Clinical profiling and medical management of Israeli individuals with Phelan McDermid syndrome
Odelia Chorin, Lior Greenbaum, Shelly Lev-Hochberg, et al.
American Journal of Human Genetics
|
February 1, 2020
Bi-allelic Variants in RALGAPA1 Cause Profound Neurodevelopmental Disability, Muscular Hypotonia, Infantile Spasms, and Feeding Abnormalities
Matias Wagner, Yuliya Skorobogatko, Ben Pode-Shakked, et al.
Molecular Genetics and Metabolism
|
August 26, 2019
Cerebral and portal vein thrombosis, macrocephaly and atypical absence seizures in Glycosylphosphatidyl inositol deficiency due to a PIGM promoter mutation
Ben Pode-Shakked, Gali Heimer, Thierry Vilboux, et al.
Page
of 6