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Genetics in Medicine : Official Journal of the American College of Medical Genetics
|
January 2, 2003
Cardiac phenotypes in chromosome 4q- syndrome with and without a deletion of the dHAND gene
Taosheng Huang, Angela E Lin, Gerald F Cox, et al.
Molecular Genetics and Metabolism
|
January 2, 2017
Long-term hematological, visceral, and growth outcomes in children with Gaucher disease type 3 treated with imiglucerase in the International Collaborative Gaucher Group Gaucher Registry
Amal El-Beshlawy, Anna Tylki-Szymanska, Ashok Vellodi, et al.
Circulation
|
January 31, 2007
Epidemiology and cause-specific outcome of hypertrophic cardiomyopathy in children: findings from the Pediatric Cardiomyopathy Registry
Steven D Colan, Steven E Lipshultz, April M Lowe, et al.
Molecular Genetics and Metabolism
|
November 14, 2017
Corrigendum to "Cause of death in patients with chronic visceral and chronic neurovisceral acid sphingomyelinase deficiency (Niemann-Pick disease type B and B variant): Literature review and report of new cases" [Mol. Genet. Metab. 118 (2016) 206-213]
David Cassiman, Seymour Packman, Bruno Bembi, et al.
Molecular Genetics and Metabolism
|
May 21, 2016
Cause of death in patients with chronic visceral and chronic neurovisceral acid sphingomyelinase deficiency (Niemann-Pick disease type B and B variant): Literature review and report of new cases
David Cassiman, Seymour Packman, Bruno Bembi, et al.
The Journal of Pediatrics
|
March 18, 2003
Arginase deficiency with lethal neonatal expression: evidence for the glutamine hypothesis of cerebral edema
Jonathan D Picker, Ana C Puga, Harvey L Levy, et al.
Molecular Genetics and Metabolism
|
June 8, 2015
Successful within-patient dose escalation of olipudase alfa in acid sphingomyelinase deficiency
Melissa P Wasserstein, Simon A Jones, Handrean Soran, et al.
Radiology
|
November 24, 2005
Type B Niemann-Pick disease: findings at chest radiography, thin-section CT, and pulmonary function testing
David S Mendelson, Melissa P Wasserstein, Robert J Desnick, et al.
American Heart Journal
|
September 18, 2012
Outcomes in children with Noonan syndrome and hypertrophic cardiomyopathy: a study from the Pediatric Cardiomyopathy Registry
James D Wilkinson, April M Lowe, Bonnie A Salbert, et al.
Pediatrics
|
January 2, 2009
Long-term efficacy and safety of laronidase in the treatment of mucopolysaccharidosis I
Lorne A Clarke, J Edmond Wraith, Michael Beck, et al.
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Search research articles
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Showing results (41-50 of 75) with videos related to
Sort By:
Page
of 8
Genetics in Medicine : Official Journal of the American College of Medical Genetics
|
January 2, 2003
Cardiac phenotypes in chromosome 4q- syndrome with and without a deletion of the dHAND gene
Taosheng Huang, Angela E Lin, Gerald F Cox, et al.
Molecular Genetics and Metabolism
|
January 2, 2017
Long-term hematological, visceral, and growth outcomes in children with Gaucher disease type 3 treated with imiglucerase in the International Collaborative Gaucher Group Gaucher Registry
Amal El-Beshlawy, Anna Tylki-Szymanska, Ashok Vellodi, et al.
Circulation
|
January 31, 2007
Epidemiology and cause-specific outcome of hypertrophic cardiomyopathy in children: findings from the Pediatric Cardiomyopathy Registry
Steven D Colan, Steven E Lipshultz, April M Lowe, et al.
Molecular Genetics and Metabolism
|
November 14, 2017
Corrigendum to "Cause of death in patients with chronic visceral and chronic neurovisceral acid sphingomyelinase deficiency (Niemann-Pick disease type B and B variant): Literature review and report of new cases" [Mol. Genet. Metab. 118 (2016) 206-213]
David Cassiman, Seymour Packman, Bruno Bembi, et al.
Molecular Genetics and Metabolism
|
May 21, 2016
Cause of death in patients with chronic visceral and chronic neurovisceral acid sphingomyelinase deficiency (Niemann-Pick disease type B and B variant): Literature review and report of new cases
David Cassiman, Seymour Packman, Bruno Bembi, et al.
The Journal of Pediatrics
|
March 18, 2003
Arginase deficiency with lethal neonatal expression: evidence for the glutamine hypothesis of cerebral edema
Jonathan D Picker, Ana C Puga, Harvey L Levy, et al.
Molecular Genetics and Metabolism
|
June 8, 2015
Successful within-patient dose escalation of olipudase alfa in acid sphingomyelinase deficiency
Melissa P Wasserstein, Simon A Jones, Handrean Soran, et al.
Radiology
|
November 24, 2005
Type B Niemann-Pick disease: findings at chest radiography, thin-section CT, and pulmonary function testing
David S Mendelson, Melissa P Wasserstein, Robert J Desnick, et al.
American Heart Journal
|
September 18, 2012
Outcomes in children with Noonan syndrome and hypertrophic cardiomyopathy: a study from the Pediatric Cardiomyopathy Registry
James D Wilkinson, April M Lowe, Bonnie A Salbert, et al.
Pediatrics
|
January 2, 2009
Long-term efficacy and safety of laronidase in the treatment of mucopolysaccharidosis I
Lorne A Clarke, J Edmond Wraith, Michael Beck, et al.
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of 8