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Journal of Thrombosis and Haemostasis : JTH
|
December 17, 2020
Establishment of a framework for assessing mortality in persons with congenital hemophilia A and its application to an adverse event reporting database
Steven W Pipe, Rebecca Kruse-Jarres, Johnny N Mahlangu, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy
|
July 11, 2006
Evidence of multiyear factor IX expression by AAV-mediated gene transfer to skeletal muscle in an individual with severe hemophilia B
Haiyan Jiang, Glenn F Pierce, Margareth C Ozelo, et al.
Blood
|
July 27, 2006
Effects of transient immunosuppression on adenoassociated, virus-mediated, liver-directed gene transfer in rhesus macaques and implications for human gene therapy
Haiyan Jiang, Linda B Couto, Susannah Patarroyo-White, et al.
Research and Practice in Thrombosis and Haemostasis
|
February 3, 2025
Adeno-associated virus-based gene therapy for hemophilia-addressing the gaps
Wolfgang Miesbach, Paul Batty, Pratima Chowdary, et al.
Blood
|
July 5, 2007
Modulation of tolerance to the transgene product in a nonhuman primate model of AAV-mediated gene transfer to liver
Federico Mingozzi, Nicole C Hasbrouck, Etiena Basner-Tschakarjan, et al.
Blood
|
August 6, 2009
Enhanced efficacy of recombinant FVIII in noncovalent complex with PEGylated liposome in hemophilia A mice
Junliang Pan, Tongyao Liu, Ji-Yun Kim, et al.
Blood
|
September 11, 2020
Activity of transgene-produced B-domain-deleted factor VIII in human plasma following AAV5 gene therapy
Steffen Rosen, Stefan Tiefenbacher, Mary Robinson, et al.
Haemophilia : the Official Journal of the World Federation of Hemophilia
|
February 6, 2024
Long-term safety and efficacy outcomes of valoctocogene roxaparvovec gene transfer up to 6 years post-treatment
Emily Symington, Savita Rangarajan, Will Lester, et al.
Journal of Virology
|
November 25, 2005
Novel caprine adeno-associated virus (AAV) capsid (AAV-Go.1) is closely related to the primate AAV-5 and has unique tropism and neutralization properties
Alejandra E Arbetman, Michael Lochrie, Shangzhen Zhou, et al.
Virology
|
June 30, 2006
Adeno-associated virus (AAV) capsid genes isolated from rat and mouse liver genomic DNA define two new AAV species distantly related to AAV-5
Michael A Lochrie, Gwen P Tatsuno, Alejandra E Arbetman, et al.
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of 10
Search research articles
Search
Showing results (51-60 of 92) with videos related to
Sort By:
Page
of 10
Journal of Thrombosis and Haemostasis : JTH
|
December 17, 2020
Establishment of a framework for assessing mortality in persons with congenital hemophilia A and its application to an adverse event reporting database
Steven W Pipe, Rebecca Kruse-Jarres, Johnny N Mahlangu, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy
|
July 11, 2006
Evidence of multiyear factor IX expression by AAV-mediated gene transfer to skeletal muscle in an individual with severe hemophilia B
Haiyan Jiang, Glenn F Pierce, Margareth C Ozelo, et al.
Blood
|
July 27, 2006
Effects of transient immunosuppression on adenoassociated, virus-mediated, liver-directed gene transfer in rhesus macaques and implications for human gene therapy
Haiyan Jiang, Linda B Couto, Susannah Patarroyo-White, et al.
Research and Practice in Thrombosis and Haemostasis
|
February 3, 2025
Adeno-associated virus-based gene therapy for hemophilia-addressing the gaps
Wolfgang Miesbach, Paul Batty, Pratima Chowdary, et al.
Blood
|
July 5, 2007
Modulation of tolerance to the transgene product in a nonhuman primate model of AAV-mediated gene transfer to liver
Federico Mingozzi, Nicole C Hasbrouck, Etiena Basner-Tschakarjan, et al.
Blood
|
August 6, 2009
Enhanced efficacy of recombinant FVIII in noncovalent complex with PEGylated liposome in hemophilia A mice
Junliang Pan, Tongyao Liu, Ji-Yun Kim, et al.
Blood
|
September 11, 2020
Activity of transgene-produced B-domain-deleted factor VIII in human plasma following AAV5 gene therapy
Steffen Rosen, Stefan Tiefenbacher, Mary Robinson, et al.
Haemophilia : the Official Journal of the World Federation of Hemophilia
|
February 6, 2024
Long-term safety and efficacy outcomes of valoctocogene roxaparvovec gene transfer up to 6 years post-treatment
Emily Symington, Savita Rangarajan, Will Lester, et al.
Journal of Virology
|
November 25, 2005
Novel caprine adeno-associated virus (AAV) capsid (AAV-Go.1) is closely related to the primate AAV-5 and has unique tropism and neutralization properties
Alejandra E Arbetman, Michael Lochrie, Shangzhen Zhou, et al.
Virology
|
June 30, 2006
Adeno-associated virus (AAV) capsid genes isolated from rat and mouse liver genomic DNA define two new AAV species distantly related to AAV-5
Michael A Lochrie, Gwen P Tatsuno, Alejandra E Arbetman, et al.
Page
of 10