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Therapeutic Advances in Endocrinology and Metabolism|November 14, 2012
Therapeutic approaches for lysosomal storage diseasesGregory M PastoresExpert Opinion on Biological Therapy|March 14, 2002
Advances in the management of Anderson-Fabry disease: enzyme replacement therapyGregory M Pastores, Ravi ThadhaniPediatric Endocrinology Reviews : PER|January 2, 2014
Orphan drug developmentGregory M Pastores, Punita GuptaDrugs in R&D|November 1, 2006
A chaperone-mediated approach to enzyme enhancement as a therapeutic option for the lysosomal storage disordersGregory M Pastores, Swati SathePediatric Health, Medicine and Therapeutics|February 2, 2018
Spotlight on taliglucerase alfa in the treatment of pediatric patients with type 1 Gaucher diseasePunita Gupta, Gregory M PastoresExpert Opinion on Investigational Drugs|January 31, 2003
Substrate reduction therapy: miglustat as a remedy for symptomatic patients with Gaucher disease type 1Gregory M Pastores, Natalie L BarnettCurrent Opinion in Hematology|October 31, 2012
Haematological manifestations and complications of Gaucher diseaseDerralynn A Hughes, Gregory M PastoresKidney International|January 31, 2009
To see a world in a grain of sand: elucidating the pathophysiology of Anderson-Fabry disease through investigations of a cellular modelGregory M Pastores, Derralynn A HughesDrug Design, Development and Therapy|February 28, 2020
Lysosomal Acid Lipase Deficiency: Therapeutic OptionsGregory M Pastores, Derralynn A HughesDiseases (Basel, Switzerland)|September 22, 2017
Lysosomal Storage Disorders and MalignancyGregory M Pastores, Derralynn A HughesPageof 10