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Molecular Therapy : the Journal of the American Society of Gene Therapy
|
December 20, 2014
Perforin gene transfer into hematopoietic stem cells improves immune dysregulation in murine models of perforin deficiency
Marlene Carmo, Kimberly A Risma, Paritha Arumugam, et al.
Science Translational Medicine
|
August 26, 2011
Hematopoietic stem cell gene therapy for adenosine deaminase-deficient severe combined immunodeficiency leads to long-term immunological recovery and metabolic correction
H Bobby Gaspar, Samantha Cooray, Kimberly C Gilmour, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy
|
March 22, 2012
The β-globin locus control region in combination with the EF1α short promoter allows enhanced lentiviral vector-mediated erythroid gene expression with conserved multilineage activity
Claudia A Montiel-Equihua, Lin Zhang, Sean Knight, et al.
Molecular Therapy. Methods & Clinical Development
|
August 11, 2020
Lentiviral Hematopoietic Stem Cell Gene Therapy Rescues Clinical Phenotypes in a Murine Model of Pompe Disease
Giuseppa Piras, Claudia Montiel-Equihua, Yee-Ka Agnes Chan, et al.
Lancet (London, England)
|
September 5, 2009
Haemopoietic stem-cell transplantation with antibody-based minimal-intensity conditioning: a phase 1/2 study
Karin C Straathof, Kanchan Rao, Matthias Eyrich, et al.
Bone Marrow Transplantation
|
April 16, 2013
Hematopoietic SCT in Europe: data and trends in 2011
J R Passweg, H Baldomero, M Bregni, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy
|
August 15, 2006
Successful reconstitution of immunity in ADA-SCID by stem cell gene therapy following cessation of PEG-ADA and use of mild preconditioning
H Bobby Gaspar, Emma Bjorkegren, Kate Parsley, et al.
Blood
|
June 3, 2006
Adoptive immunotherapy with allodepleted donor T-cells improves immune reconstitution after haploidentical stem cell transplantation
Persis J Amrolia, Giada Muccioli-Casadei, Helen Huls, et al.
Plos Biology
|
November 10, 2011
Molecular pathogenesis of EBV susceptibility in XLP as revealed by analysis of female carriers with heterozygous expression of SAP
Umaimainthan Palendira, Carol Low, Anna Chan, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy
|
March 29, 2024
Anti-CD45 PBD-based antibody-drug conjugates are effective targeted conditioning agents for gene therapy and stem cell transplant
Jenny Yeung, Aiyin Liao, Matthew Shaw, et al.
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of 12
Search research articles
Search
Showing results (71-80 of 115) with videos related to
Sort By:
Page
of 12
Molecular Therapy : the Journal of the American Society of Gene Therapy
|
December 20, 2014
Perforin gene transfer into hematopoietic stem cells improves immune dysregulation in murine models of perforin deficiency
Marlene Carmo, Kimberly A Risma, Paritha Arumugam, et al.
Science Translational Medicine
|
August 26, 2011
Hematopoietic stem cell gene therapy for adenosine deaminase-deficient severe combined immunodeficiency leads to long-term immunological recovery and metabolic correction
H Bobby Gaspar, Samantha Cooray, Kimberly C Gilmour, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy
|
March 22, 2012
The β-globin locus control region in combination with the EF1α short promoter allows enhanced lentiviral vector-mediated erythroid gene expression with conserved multilineage activity
Claudia A Montiel-Equihua, Lin Zhang, Sean Knight, et al.
Molecular Therapy. Methods & Clinical Development
|
August 11, 2020
Lentiviral Hematopoietic Stem Cell Gene Therapy Rescues Clinical Phenotypes in a Murine Model of Pompe Disease
Giuseppa Piras, Claudia Montiel-Equihua, Yee-Ka Agnes Chan, et al.
Lancet (London, England)
|
September 5, 2009
Haemopoietic stem-cell transplantation with antibody-based minimal-intensity conditioning: a phase 1/2 study
Karin C Straathof, Kanchan Rao, Matthias Eyrich, et al.
Bone Marrow Transplantation
|
April 16, 2013
Hematopoietic SCT in Europe: data and trends in 2011
J R Passweg, H Baldomero, M Bregni, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy
|
August 15, 2006
Successful reconstitution of immunity in ADA-SCID by stem cell gene therapy following cessation of PEG-ADA and use of mild preconditioning
H Bobby Gaspar, Emma Bjorkegren, Kate Parsley, et al.
Blood
|
June 3, 2006
Adoptive immunotherapy with allodepleted donor T-cells improves immune reconstitution after haploidentical stem cell transplantation
Persis J Amrolia, Giada Muccioli-Casadei, Helen Huls, et al.
Plos Biology
|
November 10, 2011
Molecular pathogenesis of EBV susceptibility in XLP as revealed by analysis of female carriers with heterozygous expression of SAP
Umaimainthan Palendira, Carol Low, Anna Chan, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy
|
March 29, 2024
Anti-CD45 PBD-based antibody-drug conjugates are effective targeted conditioning agents for gene therapy and stem cell transplant
Jenny Yeung, Aiyin Liao, Matthew Shaw, et al.
Page
of 12