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Progress in Molecular Biology and Translational Science
|
June 27, 2021
Genome editing in mucopolysaccharidoses and mucolipidoses
Hallana Souza Santos, Edina Poletto, Roselena Schuh, et al.
Frontiers in Cardiovascular Medicine
|
January 31, 2022
Progression of Cardiovascular Manifestations in Adults and Children With Mucopolysaccharidoses With and Without Enzyme Replacement Therapy
Fabiano de Oliveira Poswar, Hallana Souza Santos, Angela Barreto Santiago Santos, et al.
Current Gene Therapy
|
May 5, 2021
In Situ Gene Therapy
Hallana Souza Santos, Luiza Rodrigues, Luisa Natalia Pimentel Vera, et al.
Pharmaceutics
|
March 28, 2026
Liposomal CRISPR/Cas9-Mediated Local Genome Editing for Joint Disease in Mucopolysaccharidosis Type I
Hallana Souza Santos, Edina Poletto, Luisa Natalia Pimentel Vera, et al.
International Journal of Pharmaceutics
|
June 19, 2024
Laronidase-loaded liposomes reach the brain and other hard-to-treat organs after noninvasive nasal administration
Roselena Silvestri Schuh, Eduarda Piovesan Franceschi, Bruna Brazeiro Brum, et al.
Page
of 1
Search research articles
Search
Showing results (1-10 of 5) with videos related to
Sort By:
Page
of 1
Progress in Molecular Biology and Translational Science
|
June 27, 2021
Genome editing in mucopolysaccharidoses and mucolipidoses
Hallana Souza Santos, Edina Poletto, Roselena Schuh, et al.
Frontiers in Cardiovascular Medicine
|
January 31, 2022
Progression of Cardiovascular Manifestations in Adults and Children With Mucopolysaccharidoses With and Without Enzyme Replacement Therapy
Fabiano de Oliveira Poswar, Hallana Souza Santos, Angela Barreto Santiago Santos, et al.
Current Gene Therapy
|
May 5, 2021
In Situ Gene Therapy
Hallana Souza Santos, Luiza Rodrigues, Luisa Natalia Pimentel Vera, et al.
Pharmaceutics
|
March 28, 2026
Liposomal CRISPR/Cas9-Mediated Local Genome Editing for Joint Disease in Mucopolysaccharidosis Type I
Hallana Souza Santos, Edina Poletto, Luisa Natalia Pimentel Vera, et al.
International Journal of Pharmaceutics
|
June 19, 2024
Laronidase-loaded liposomes reach the brain and other hard-to-treat organs after noninvasive nasal administration
Roselena Silvestri Schuh, Eduarda Piovesan Franceschi, Bruna Brazeiro Brum, et al.
Page
of 1