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The Lancet. Child & Adolescent Health
|
November 10, 2021
Gene replacement therapy with onasemnogene abeparvovec in children with spinal muscular atrophy aged 24 months or younger and bodyweight up to 15 kg: an observational cohort study
Claudia Weiß, Andreas Ziegler, Lena-Luise Becker, et al.
Epilepsia
|
September 1, 2023
Treatment of seizures in the neonate: Guidelines and consensus-based recommendations-Special report from the ILAE Task Force on Neonatal Seizures
Ronit M Pressler, Nicholas S Abend, Stéphan Auvin, et al.
Movement Disorders : Official Journal of the Movement Disorder Society
|
December 30, 2021
Quality of Life After Deep Brain Stimulation of Pediatric Patients with Dyskinetic Cerebral Palsy: A Prospective, Single-Arm, Multicenter Study with a Subsequent Randomized Double-Blind Crossover (STIM-CP)
Anne Koy, Andrea A Kühn, Julius Huebl, et al.
Expert Review of Clinical Pharmacology
|
April 1, 2021
Prescription patterns of antiseizure drugs in tuberous sclerosis complex (TSC)-associated epilepsy: a multicenter cohort study from Germany and review of the literature
Adam Strzelczyk, Janina Grau, Thomas Bast, et al.
Journal of Neuromuscular Diseases
|
December 4, 2022
Newbornscreening SMA - From Pilot Project to Nationwide Screening in Germany
Wolfgang Müller-Felber, Astrid Blaschek, Oliver Schwartz, et al.
Orphanet Journal of Rare Diseases
|
June 22, 2021
Direct and indirect costs and cost-driving factors of Tuberous sclerosis complex in children, adolescents, and caregivers: a multicenter cohort study
Janina Grau, Johann Philipp Zöllner, Susanne Schubert-Bast, et al.
European Journal of Paediatric Neurology : EJPN : Official Journal of the European Paediatric Neurology Society
|
October 21, 2021
Health-related quality of life in children and adolescents with tuberous sclerosis complex and their caregivers: A multicentre cohort study from Germany
Laurent M Willems, Susanne Schubert-Bast, Janina Grau, et al.
CNS Drugs
|
July 18, 2021
Efficacy, Retention and Tolerability of Everolimus in Patients with Tuberous Sclerosis Complex: A Survey-Based Study on Patients' Perspectives
Laurent M Willems, Felix Rosenow, Susanne Schubert-Bast, et al.
Journal of Neuromuscular Diseases
|
November 24, 2025
Delphi consensus on gene therapy of spinal muscular atrophy with onasemnogene abeparvovec in Germany, Austria and Switzerland-part I-systematic literature review and existing evidence
Claudia Weiß, Katharina Vill, Matthias Baumann, et al.
American Journal of Human Genetics
|
November 8, 2018
Bi-allelic ADPRHL2 Mutations Cause Neurodegeneration with Developmental Delay, Ataxia, and Axonal Neuropathy
Katharina Danhauser, Bader Alhaddad, Christine Makowski, et al.
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of 9
Search research articles
Search
Showing results (71-80 of 83) with videos related to
Sort By:
Page
of 9
The Lancet. Child & Adolescent Health
|
November 10, 2021
Gene replacement therapy with onasemnogene abeparvovec in children with spinal muscular atrophy aged 24 months or younger and bodyweight up to 15 kg: an observational cohort study
Claudia Weiß, Andreas Ziegler, Lena-Luise Becker, et al.
Epilepsia
|
September 1, 2023
Treatment of seizures in the neonate: Guidelines and consensus-based recommendations-Special report from the ILAE Task Force on Neonatal Seizures
Ronit M Pressler, Nicholas S Abend, Stéphan Auvin, et al.
Movement Disorders : Official Journal of the Movement Disorder Society
|
December 30, 2021
Quality of Life After Deep Brain Stimulation of Pediatric Patients with Dyskinetic Cerebral Palsy: A Prospective, Single-Arm, Multicenter Study with a Subsequent Randomized Double-Blind Crossover (STIM-CP)
Anne Koy, Andrea A Kühn, Julius Huebl, et al.
Expert Review of Clinical Pharmacology
|
April 1, 2021
Prescription patterns of antiseizure drugs in tuberous sclerosis complex (TSC)-associated epilepsy: a multicenter cohort study from Germany and review of the literature
Adam Strzelczyk, Janina Grau, Thomas Bast, et al.
Journal of Neuromuscular Diseases
|
December 4, 2022
Newbornscreening SMA - From Pilot Project to Nationwide Screening in Germany
Wolfgang Müller-Felber, Astrid Blaschek, Oliver Schwartz, et al.
Orphanet Journal of Rare Diseases
|
June 22, 2021
Direct and indirect costs and cost-driving factors of Tuberous sclerosis complex in children, adolescents, and caregivers: a multicenter cohort study
Janina Grau, Johann Philipp Zöllner, Susanne Schubert-Bast, et al.
European Journal of Paediatric Neurology : EJPN : Official Journal of the European Paediatric Neurology Society
|
October 21, 2021
Health-related quality of life in children and adolescents with tuberous sclerosis complex and their caregivers: A multicentre cohort study from Germany
Laurent M Willems, Susanne Schubert-Bast, Janina Grau, et al.
CNS Drugs
|
July 18, 2021
Efficacy, Retention and Tolerability of Everolimus in Patients with Tuberous Sclerosis Complex: A Survey-Based Study on Patients' Perspectives
Laurent M Willems, Felix Rosenow, Susanne Schubert-Bast, et al.
Journal of Neuromuscular Diseases
|
November 24, 2025
Delphi consensus on gene therapy of spinal muscular atrophy with onasemnogene abeparvovec in Germany, Austria and Switzerland-part I-systematic literature review and existing evidence
Claudia Weiß, Katharina Vill, Matthias Baumann, et al.
American Journal of Human Genetics
|
November 8, 2018
Bi-allelic ADPRHL2 Mutations Cause Neurodegeneration with Developmental Delay, Ataxia, and Axonal Neuropathy
Katharina Danhauser, Bader Alhaddad, Christine Makowski, et al.
Page
of 9