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Journal of Inherited Metabolic Disease|June 9, 2020
A primer to gene therapy: Progress, prospects, and problemsHidde A Zittersteijn, Manuel A F V Gonçalves, Rob C HoebenFrontiers in Genome Editing|October 29, 2021
A Small Key for a Heavy Door: Genetic Therapies for the Treatment of HemoglobinopathiesHidde A Zittersteijn, Cornelis L Harteveld, Stefanie Klaver-Flores, et al.Frontiers in Genome Editing|October 29, 2021
Genomic Engineering in Human Hematopoietic Stem Cells: Hype or Hope?Stefanie Klaver-Flores, Hidde A Zittersteijn, Kirsten Canté-Barrett, et al.Stem Cell Research & Therapy|January 30, 2021
Generation of dyskeratosis congenita-like hematopoietic stem cells through the stable inhibition of DKC1Carlos Carrascoso-Rubio, Hidde A Zittersteijn, Laura Pintado-Berninches, et al.Gene Therapy|January 5, 2020
Integrating gene delivery and gene-editing technologies by adenoviral vector transfer of optimized CRISPR-Cas9 componentsIgnazio Maggio, Hidde A Zittersteijn, Qian Wang, et al.Pageof 1