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Neurology. Genetics
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February 12, 2020
Clinical spectrum of POLR3-related leukodystrophy caused by biallelic <i>POLR1C</i> pathogenic variants
Laurence Gauquelin, Ferdy K Cayami, László Sztriha, et al.
Neurology
|
August 22, 2024
Framework for Multistakeholder Patient Registries in the Field of Rare Diseases: Focus on Neurogenetic Diseases
Daphne H Schoenmakers, Sibren van den Berg, Lonneke Timmers, et al.
Molecular Genetics and Metabolism
|
September 3, 2017
Revised consensus statement on the preventive and symptomatic care of patients with leukodystrophies
Laura A Adang, Omar Sherbini, Laura Ball, et al.
European Journal of Paediatric Neurology : EJPN : Official Journal of the European Paediatric Neurology Society
|
June 7, 2025
Key lessons from the first international treatment eligibility committee: the case of metachromatic leukodystrophy
Daphne H Schoenmakers, Marije A B C Asbreuk, Tamara Martin, et al.
American Journal of Human Genetics
|
May 31, 2016
Loss-of-Function Mutations in FRRS1L Lead to an Epileptic-Dyskinetic Encephalopathy
Marianna Madeo, Michelle Stewart, Yuyang Sun, et al.
Nature Communications
|
April 3, 2023
Cellular differentiation into hyphae and spores in halophilic archaea
Shu-Kun Tang, Xiao-Yang Zhi, Yao Zhang, et al.
Neurology
|
November 13, 2025
Consensus-Based Expert Recommendations for Diagnosis and Clinical Management of Vanishing White Matter
Romy J van Voorst, Daphne H Schoenmakers, Joshua L Bonkowsky, et al.
American Journal of Human Genetics
|
March 25, 2023
Bi-allelic SNAPC4 variants dysregulate global alternative splicing and lead to neuroregression and progressive spastic paraparesis
F Graeme Frost, Marie Morimoto, Prashant Sharma, et al.
Molecular Genetics and Metabolism
|
February 14, 2025
The natural history of variable subtypes in pediatric-onset TUBB4A-related leukodystrophy
Francesco Gavazzi, Brittany Charsar, Eline Hamilton, et al.
Brain : a Journal of Neurology
|
August 20, 2021
Biallelic PI4KA variants cause neurological, intestinal and immunological disease
Claire G Salter, Yiying Cai, Bernice Lo, et al.
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of 90
Search research articles
Search
Showing results (871-880 of 898) with videos related to
Sort By:
Page
of 90
Neurology. Genetics
|
February 12, 2020
Clinical spectrum of POLR3-related leukodystrophy caused by biallelic <i>POLR1C</i> pathogenic variants
Laurence Gauquelin, Ferdy K Cayami, László Sztriha, et al.
Neurology
|
August 22, 2024
Framework for Multistakeholder Patient Registries in the Field of Rare Diseases: Focus on Neurogenetic Diseases
Daphne H Schoenmakers, Sibren van den Berg, Lonneke Timmers, et al.
Molecular Genetics and Metabolism
|
September 3, 2017
Revised consensus statement on the preventive and symptomatic care of patients with leukodystrophies
Laura A Adang, Omar Sherbini, Laura Ball, et al.
European Journal of Paediatric Neurology : EJPN : Official Journal of the European Paediatric Neurology Society
|
June 7, 2025
Key lessons from the first international treatment eligibility committee: the case of metachromatic leukodystrophy
Daphne H Schoenmakers, Marije A B C Asbreuk, Tamara Martin, et al.
American Journal of Human Genetics
|
May 31, 2016
Loss-of-Function Mutations in FRRS1L Lead to an Epileptic-Dyskinetic Encephalopathy
Marianna Madeo, Michelle Stewart, Yuyang Sun, et al.
Nature Communications
|
April 3, 2023
Cellular differentiation into hyphae and spores in halophilic archaea
Shu-Kun Tang, Xiao-Yang Zhi, Yao Zhang, et al.
Neurology
|
November 13, 2025
Consensus-Based Expert Recommendations for Diagnosis and Clinical Management of Vanishing White Matter
Romy J van Voorst, Daphne H Schoenmakers, Joshua L Bonkowsky, et al.
American Journal of Human Genetics
|
March 25, 2023
Bi-allelic SNAPC4 variants dysregulate global alternative splicing and lead to neuroregression and progressive spastic paraparesis
F Graeme Frost, Marie Morimoto, Prashant Sharma, et al.
Molecular Genetics and Metabolism
|
February 14, 2025
The natural history of variable subtypes in pediatric-onset TUBB4A-related leukodystrophy
Francesco Gavazzi, Brittany Charsar, Eline Hamilton, et al.
Brain : a Journal of Neurology
|
August 20, 2021
Biallelic PI4KA variants cause neurological, intestinal and immunological disease
Claire G Salter, Yiying Cai, Bernice Lo, et al.
Page
of 90