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Journal of Neurology, Neurosurgery, and Psychiatry|September 12, 2020
Nusinersen safety and effects on motor function in adult spinal muscular atrophy type 2 and 3Lorenzo Maggi, Luca Bello, Silvia Bonanno, et al.
Journal of Neurology, Neurosurgery, and Psychiatry|October 11, 2022
Adults with spinal muscular atrophy: a large-scale natural history study shows gender effect on diseaseLorenzo Maggi, Luca Bello, Silvia Bonanno, et al.
Muscle & Nerve|August 3, 2024
Six-minute walk test as outcome measure of fatigability in adults with spinal muscular atrophy treated with nusinersenAlessandra Govoni, Giulia Ricci, Silvia Bonanno, et al.
European Journal of Neurology|September 23, 2022
Effect of RNS60 in amyotrophic lateral sclerosis: a phase II multicentre, randomized, double-blind, placebo-controlled trialEttore Beghi, Elisabetta Pupillo, Elisa Bianchi, et al.
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