Showing results (201-210 of 319) with videos related to

Sort By:
Pageof 32
Molecular Therapy. Methods & Clinical Development|March 26, 2021
Anti-CD19 CARs displayed at the surface of lentiviral vector particles promote transduction of target-expressing cellsNicole Cordes, Carolin Kolbe, Dominik Lock, et al.
Communications Biology|October 9, 2024
Gene editing of NCF1 loci is associated with homologous recombination and chromosomal rearrangementsFederica Raimondi, Kah Mun Siow, Dominik Wrona, et al.
Neurology and Therapy|February 13, 2023
Risdiplam in Patients Previously Treated with Other Therapies for Spinal Muscular Atrophy: An Interim Analysis from the JEWELFISH StudyClaudia A Chiriboga, Claudio Bruno, Tina Duong, et al.
Haematologica|December 16, 2017
Variable impairment of platelet functions in patients with severe, genetically linked immune deficienciesMagdolna Nagy, Tom G Mastenbroek, Nadine J A Mattheij, et al.
Molecular Therapy. Nucleic Acids|August 30, 2021
A non-viral and selection-free COL7A1 HDR approach with improved safety profile for dystrophic epidermolysis bullosaThomas Kocher, Johannes Bischof, Simone Alexandra Haas, et al.
Frontiers in Immunology|March 4, 2024
Artificial Targets: a versatile cell-free platform to characterize CAR T cell function in vitroXueting Wang, Nicholas J A Tokarew, Nadine Borgelt, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy|November 19, 2025
Base edited skin equivalents with clinical potential for ex vivo correction of recessive dystrophic epidermolysis bullosaAlex Bassons-Bascuñana, Blanca Duarte, Estela Méndez-Jiménez, et al.
Nature Communications|May 8, 2026
Simultaneous orthogonal cell engineering by a single CRISPR-Cas9 polyfunctional editorDeborah Cipria, Tania Baccega, Miriana Rizzo, et al.
Acta Neuropathologica|December 24, 2013
Myopathy in Marinesco-Sjögren syndrome links endoplasmic reticulum chaperone dysfunction to nuclear envelope pathologyAndreas Roos, Stephan Buchkremer, Laxmikanth Kollipara, et al.
Neurology. Genetics|April 12, 2016
Respiratory chain deficiency in nonmitochondrial diseaseAngela Pyle, Helen J Nightingale, Helen Griffin, et al.
Pageof 32