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Molecular Genetics and Metabolism
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September 12, 2024
Developing a scoring system for gene curation prioritization in lysosomal diseases
Matheus Vernet Machado Bressan Wilke, Jennifer Goldstein, Emily Groopman, et al.
Genetics in Medicine : Official Journal of the American College of Medical Genetics
|
March 6, 2015
CRIM-negative infantile Pompe disease: characterization of immune responses in patients treated with ERT monotherapy
Kathryn L Berrier, Zoheb B Kazi, Sean N Prater, et al.
Genetics in Medicine : Official Journal of the American College of Medical Genetics
|
July 3, 2015
CORRIGENDUM: CRIM-negative infantile Pompe disease: characterization of immune responses in patients treated with ERT monotherapy
Kathryn L Berrier, Zoheb B Kazi, Sean N Prater, et al.
Genetics in Medicine : Official Journal of the American College of Medical Genetics
|
January 20, 2019
Diagnosis and management of glycogen storage diseases type VI and IX: a clinical practice resource of the American College of Medical Genetics and Genomics (ACMG)
Priya S Kishnani, Jennifer Goldstein, Stephanie L Austin, et al.
Medrxiv : the Preprint Server for Health Sciences
|
August 30, 2024
Assessment of genes involved in lysosomal diseases using the ClinGen Clinical Validity framework
Emily Groopman, Shruthi Mohan, Amber Waddell, et al.
Molecular Genetics and Metabolism
|
October 19, 2024
Assessment of genes involved in lysosomal diseases using the ClinGen clinical validity framework
Emily Groopman, Shruthi Mohan, Amber Waddell, et al.
Metabolic Brain Disease
|
February 14, 2018
Treatment outcome of creatine transporter deficiency: international retrospective cohort study
Theodora U J Bruun, Sarah Sidky, Anabela O Bandeira, et al.
Circulation. Genomic and Precision Medicine
|
January 26, 2019
Evaluating the Clinical Validity of Hypertrophic Cardiomyopathy Genes
Jodie Ingles, Jennifer Goldstein, Courtney Thaxton, et al.
European Journal of Paediatric Neurology : EJPN : Official Journal of the European Paediatric Neurology Society
|
March 7, 2018
Treatment outcome of twenty-two patients with guanidinoacetate methyltransferase deficiency: An international retrospective cohort study
Yannay Khaikin, Sarah Sidky, Jose Abdenur, et al.
Genetics in Medicine : Official Journal of the American College of Medical Genetics
|
January 16, 2015
Whole-exome sequencing in undiagnosed genetic diseases: interpreting 119 trios
Xiaolin Zhu, Slavé Petrovski, Pingxing Xie, et al.
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of 4
Search research articles
Search
Showing results (21-30 of 32) with videos related to
Sort By:
Page
of 4
Molecular Genetics and Metabolism
|
September 12, 2024
Developing a scoring system for gene curation prioritization in lysosomal diseases
Matheus Vernet Machado Bressan Wilke, Jennifer Goldstein, Emily Groopman, et al.
Genetics in Medicine : Official Journal of the American College of Medical Genetics
|
March 6, 2015
CRIM-negative infantile Pompe disease: characterization of immune responses in patients treated with ERT monotherapy
Kathryn L Berrier, Zoheb B Kazi, Sean N Prater, et al.
Genetics in Medicine : Official Journal of the American College of Medical Genetics
|
July 3, 2015
CORRIGENDUM: CRIM-negative infantile Pompe disease: characterization of immune responses in patients treated with ERT monotherapy
Kathryn L Berrier, Zoheb B Kazi, Sean N Prater, et al.
Genetics in Medicine : Official Journal of the American College of Medical Genetics
|
January 20, 2019
Diagnosis and management of glycogen storage diseases type VI and IX: a clinical practice resource of the American College of Medical Genetics and Genomics (ACMG)
Priya S Kishnani, Jennifer Goldstein, Stephanie L Austin, et al.
Medrxiv : the Preprint Server for Health Sciences
|
August 30, 2024
Assessment of genes involved in lysosomal diseases using the ClinGen Clinical Validity framework
Emily Groopman, Shruthi Mohan, Amber Waddell, et al.
Molecular Genetics and Metabolism
|
October 19, 2024
Assessment of genes involved in lysosomal diseases using the ClinGen clinical validity framework
Emily Groopman, Shruthi Mohan, Amber Waddell, et al.
Metabolic Brain Disease
|
February 14, 2018
Treatment outcome of creatine transporter deficiency: international retrospective cohort study
Theodora U J Bruun, Sarah Sidky, Anabela O Bandeira, et al.
Circulation. Genomic and Precision Medicine
|
January 26, 2019
Evaluating the Clinical Validity of Hypertrophic Cardiomyopathy Genes
Jodie Ingles, Jennifer Goldstein, Courtney Thaxton, et al.
European Journal of Paediatric Neurology : EJPN : Official Journal of the European Paediatric Neurology Society
|
March 7, 2018
Treatment outcome of twenty-two patients with guanidinoacetate methyltransferase deficiency: An international retrospective cohort study
Yannay Khaikin, Sarah Sidky, Jose Abdenur, et al.
Genetics in Medicine : Official Journal of the American College of Medical Genetics
|
January 16, 2015
Whole-exome sequencing in undiagnosed genetic diseases: interpreting 119 trios
Xiaolin Zhu, Slavé Petrovski, Pingxing Xie, et al.
Page
of 4