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Jenny McIntosh

Showing results (21-30 of 30) with videos related to

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Blood|December 3, 2011
AAV-mediated gene transfer in the perinatal period results in expression of FVII at levels that protect against fatal spontaneous hemorrhageChristopher Binny, Jenny McIntosh, Marco Della Peruta, et al.
Gene Therapy|January 11, 2023
Preclinical evaluation of FLT190, a liver-directed AAV gene therapy for Fabry diseaseJey M Jeyakumar, Azadeh Kia, Lawrence C S Tam, et al.
Gene Therapy|July 20, 2018
The murine lung as a factory to produce secreted intrapulmonary and circulatory proteinsMichael C Paul-Smith, Kamila M Pytel, Jean-François Gelinas, et al.
Science Translational Medicine|August 9, 2023
Adeno-associated virus gene therapy prevents progression of kidney disease in genetic models of nephrotic syndromeWen Y Ding, Valeryia Kuzmuk, Sarah Hunter, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy|June 2, 2011
Stable human FIX expression after 0.9G intrauterine gene transfer of self-complementary adeno-associated viral vector 5 and 8 in macaquesCitra N Z Mattar, Amit C Nathwani, Simon N Waddington, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy|January 20, 2011
Long-term safety and efficacy following systemic administration of a self-complementary AAV vector encoding human FIX pseudotyped with serotype 5 and 8 capsid proteinsAmit C Nathwani, Cecilia Rosales, Jenny McIntosh, et al.
Blood|February 22, 2013
Therapeutic levels of FVIII following a single peripheral vein administration of rAAV vector encoding a novel human factor VIII variantJenny McIntosh, Peter J Lenting, Cecilia Rosales, et al.
The New England Journal of Medicine|June 11, 2025
Sustained Clinical Benefit of AAV Gene Therapy in Severe Hemophilia BUlrike M Reiss, Andrew M Davidoff, Edward G D Tuddenham, et al.
The New England Journal of Medicine|November 20, 2014
Long-term safety and efficacy of factor IX gene therapy in hemophilia BAmit C Nathwani, Ulreke M Reiss, Edward G D Tuddenham, et al.
The New England Journal of Medicine|December 14, 2011
Adenovirus-associated virus vector-mediated gene transfer in hemophilia BAmit C Nathwani, Edward G D Tuddenham, Savita Rangarajan, et al.
Pageof 3

Showing results (21-30 of 30) with videos related to

Sort By:
Pageof 3
You have reached the last page of results.This site can display upto 30 results.
Blood|December 3, 2011
AAV-mediated gene transfer in the perinatal period results in expression of FVII at levels that protect against fatal spontaneous hemorrhageChristopher Binny, Jenny McIntosh, Marco Della Peruta, et al.
Gene Therapy|January 11, 2023
Preclinical evaluation of FLT190, a liver-directed AAV gene therapy for Fabry diseaseJey M Jeyakumar, Azadeh Kia, Lawrence C S Tam, et al.
Gene Therapy|July 20, 2018
The murine lung as a factory to produce secreted intrapulmonary and circulatory proteinsMichael C Paul-Smith, Kamila M Pytel, Jean-François Gelinas, et al.
Science Translational Medicine|August 9, 2023
Adeno-associated virus gene therapy prevents progression of kidney disease in genetic models of nephrotic syndromeWen Y Ding, Valeryia Kuzmuk, Sarah Hunter, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy|June 2, 2011
Stable human FIX expression after 0.9G intrauterine gene transfer of self-complementary adeno-associated viral vector 5 and 8 in macaquesCitra N Z Mattar, Amit C Nathwani, Simon N Waddington, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy|January 20, 2011
Long-term safety and efficacy following systemic administration of a self-complementary AAV vector encoding human FIX pseudotyped with serotype 5 and 8 capsid proteinsAmit C Nathwani, Cecilia Rosales, Jenny McIntosh, et al.
Blood|February 22, 2013
Therapeutic levels of FVIII following a single peripheral vein administration of rAAV vector encoding a novel human factor VIII variantJenny McIntosh, Peter J Lenting, Cecilia Rosales, et al.
The New England Journal of Medicine|June 11, 2025
Sustained Clinical Benefit of AAV Gene Therapy in Severe Hemophilia BUlrike M Reiss, Andrew M Davidoff, Edward G D Tuddenham, et al.
The New England Journal of Medicine|November 20, 2014
Long-term safety and efficacy of factor IX gene therapy in hemophilia BAmit C Nathwani, Ulreke M Reiss, Edward G D Tuddenham, et al.
The New England Journal of Medicine|December 14, 2011
Adenovirus-associated virus vector-mediated gene transfer in hemophilia BAmit C Nathwani, Edward G D Tuddenham, Savita Rangarajan, et al.
Pageof 3