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Molecular Genetics and Metabolism
|
August 26, 2022
Management of early treated adolescents and young adults with phenylketonuria: Development of international consensus recommendations using a modified Delphi approach
Barbara K Burton, Álvaro Hermida, Amaya Bélanger-Quintana, et al.
Journal of Medical Genetics
|
January 27, 2019
Diagnosis of 'possible' mitochondrial disease: an existential crisis
Sumit Parikh, Amel Karaa, Amy Goldstein, et al.
Oncotarget
|
April 23, 2016
Abnormal lipid processing but normal long-term repopulation potential of myc-/- hepatocytes
Lia R Edmunds, P Anthony Otero, Lokendra Sharma, et al.
Molecular Genetics and Metabolism
|
August 23, 2015
Self-reported treatment-associated symptoms among patients with urea cycle disorders participating in glycerol phenylbutyrate clinical trials
Sandesh C S Nagamani, George A Diaz, William Rhead, et al.
Genetics in Medicine : Official Journal of the American College of Medical Genetics
|
January 7, 2020
Efficacy and safety of D,L-3-hydroxybutyrate (D,L-3-HB) treatment in multiple acyl-CoA dehydrogenase deficiency
Willemijn J van Rijt, Emmalie A Jager, Derk P Allersma, et al.
Journal of Clinical Immunology
|
January 1, 2022
Prevalence of Pathogenic and Potentially Pathogenic Inborn Error of Immunity Associated Variants in Children with Severe Sepsis
Kate F Kernan, Lina Ghaloul-Gonzalez, Jerry Vockley, et al.
JCI Insight
|
October 15, 2020
A porcine model of phenylketonuria generated by CRISPR/Cas9 genome editing
Erik A Koppes, Bethany K Redel, Marie A Johnson, et al.
Genetics in Medicine : Official Journal of the American College of Medical Genetics
|
December 16, 2014
Blood ammonia and glutamine as predictors of hyperammonemic crises in patients with urea cycle disorder
Brendan Lee, George A Diaz, William Rhead, et al.
Journal of Inherited Metabolic Disease
|
November 7, 2015
Recurrent acute liver failure due to NBAS deficiency: phenotypic spectrum, disease mechanisms, and therapeutic concepts
Christian Staufner, Tobias B Haack, Marlies G Köpke, et al.
American Journal of Human Genetics
|
June 16, 2015
Biallelic Mutations in NBAS Cause Recurrent Acute Liver Failure with Onset in Infancy
Tobias B Haack, Christian Staufner, Marlies G Köpke, et al.
Page
of 30
Search research articles
Search
Showing results (271-280 of 295) with videos related to
Sort By:
Page
of 30
Molecular Genetics and Metabolism
|
August 26, 2022
Management of early treated adolescents and young adults with phenylketonuria: Development of international consensus recommendations using a modified Delphi approach
Barbara K Burton, Álvaro Hermida, Amaya Bélanger-Quintana, et al.
Journal of Medical Genetics
|
January 27, 2019
Diagnosis of 'possible' mitochondrial disease: an existential crisis
Sumit Parikh, Amel Karaa, Amy Goldstein, et al.
Oncotarget
|
April 23, 2016
Abnormal lipid processing but normal long-term repopulation potential of myc-/- hepatocytes
Lia R Edmunds, P Anthony Otero, Lokendra Sharma, et al.
Molecular Genetics and Metabolism
|
August 23, 2015
Self-reported treatment-associated symptoms among patients with urea cycle disorders participating in glycerol phenylbutyrate clinical trials
Sandesh C S Nagamani, George A Diaz, William Rhead, et al.
Genetics in Medicine : Official Journal of the American College of Medical Genetics
|
January 7, 2020
Efficacy and safety of D,L-3-hydroxybutyrate (D,L-3-HB) treatment in multiple acyl-CoA dehydrogenase deficiency
Willemijn J van Rijt, Emmalie A Jager, Derk P Allersma, et al.
Journal of Clinical Immunology
|
January 1, 2022
Prevalence of Pathogenic and Potentially Pathogenic Inborn Error of Immunity Associated Variants in Children with Severe Sepsis
Kate F Kernan, Lina Ghaloul-Gonzalez, Jerry Vockley, et al.
JCI Insight
|
October 15, 2020
A porcine model of phenylketonuria generated by CRISPR/Cas9 genome editing
Erik A Koppes, Bethany K Redel, Marie A Johnson, et al.
Genetics in Medicine : Official Journal of the American College of Medical Genetics
|
December 16, 2014
Blood ammonia and glutamine as predictors of hyperammonemic crises in patients with urea cycle disorder
Brendan Lee, George A Diaz, William Rhead, et al.
Journal of Inherited Metabolic Disease
|
November 7, 2015
Recurrent acute liver failure due to NBAS deficiency: phenotypic spectrum, disease mechanisms, and therapeutic concepts
Christian Staufner, Tobias B Haack, Marlies G Köpke, et al.
American Journal of Human Genetics
|
June 16, 2015
Biallelic Mutations in NBAS Cause Recurrent Acute Liver Failure with Onset in Infancy
Tobias B Haack, Christian Staufner, Marlies G Köpke, et al.
Page
of 30