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Journal of Neuromuscular Diseases
|
November 11, 2019
Spinal Muscular Atrophy (SMA) Subtype Concordance in Siblings: Findings From the Cure SMA Cohort
Cynthia C Jones, Suzanne F Cook, Jill Jarecki, et al.
Clinical Trials (London, England)
|
February 25, 2018
Barriers and facilitators to clinical trial participation among parents of children with pediatric neuromuscular disorders
Holly L Peay, Barbara B Biesecker, Benjamin S Wilfond, et al.
Prenatal Diagnosis
|
August 27, 2022
Investigating attitudes toward prenatal diagnosis and fetal therapy for spinal muscular atrophy
Marisa E Schwab, Shirley Shao, Li Zhang, et al.
Journal of Neuromuscular Diseases
|
April 5, 2018
An overview of the Cure SMA membership database: Highlights of key demographic and clinical characteristics of SMA members
Lisa Belter, Suzanne F Cook, Thomas O Crawford, et al.
Assay and Drug Development Technologies
|
August 23, 2014
Assays for the identification and prioritization of drug candidates for spinal muscular atrophy
Jonathan J Cherry, Dione T Kobayashi, Maureen M Lynes, et al.
Journal of Neuromuscular Diseases
|
October 26, 2020
The Cure SMA Membership Surveys: Highlights of Key Demographic and Clinical Characteristics of Individuals with Spinal Muscular Atrophy
Lisa Belter, Jill Jarecki, Sandra P Reyna, et al.
Journal of Neuromuscular Diseases
|
July 17, 2023
Identifying Biomarkers of Spinal Muscular Atrophy for Further Development
Jacqueline Glascock, Basil T Darras, Thomas O Crawford, et al.
Journal of Neuromuscular Diseases
|
April 5, 2018
Treatment Algorithm for Infants Diagnosed with Spinal Muscular Atrophy through Newborn Screening
Jacqueline Glascock, Jacinda Sampson, Amanda Haidet-Phillips, et al.
Annals of Neurology
|
November 5, 2003
Valproic acid increases SMN levels in spinal muscular atrophy patient cells
Charlotte J Sumner, Thanh N Huynh, Jennifer A Markowitz, et al.
Human Molecular Genetics
|
November 10, 2009
Effects of 2,4-diaminoquinazoline derivatives on SMN expression and phenotype in a mouse model for spinal muscular atrophy
Matthew E R Butchbach, Jasbir Singh, Margrét Thorsteinsdóttir, et al.
Page
of 4
Search research articles
Search
Showing results (21-30 of 35) with videos related to
Sort By:
Page
of 4
Journal of Neuromuscular Diseases
|
November 11, 2019
Spinal Muscular Atrophy (SMA) Subtype Concordance in Siblings: Findings From the Cure SMA Cohort
Cynthia C Jones, Suzanne F Cook, Jill Jarecki, et al.
Clinical Trials (London, England)
|
February 25, 2018
Barriers and facilitators to clinical trial participation among parents of children with pediatric neuromuscular disorders
Holly L Peay, Barbara B Biesecker, Benjamin S Wilfond, et al.
Prenatal Diagnosis
|
August 27, 2022
Investigating attitudes toward prenatal diagnosis and fetal therapy for spinal muscular atrophy
Marisa E Schwab, Shirley Shao, Li Zhang, et al.
Journal of Neuromuscular Diseases
|
April 5, 2018
An overview of the Cure SMA membership database: Highlights of key demographic and clinical characteristics of SMA members
Lisa Belter, Suzanne F Cook, Thomas O Crawford, et al.
Assay and Drug Development Technologies
|
August 23, 2014
Assays for the identification and prioritization of drug candidates for spinal muscular atrophy
Jonathan J Cherry, Dione T Kobayashi, Maureen M Lynes, et al.
Journal of Neuromuscular Diseases
|
October 26, 2020
The Cure SMA Membership Surveys: Highlights of Key Demographic and Clinical Characteristics of Individuals with Spinal Muscular Atrophy
Lisa Belter, Jill Jarecki, Sandra P Reyna, et al.
Journal of Neuromuscular Diseases
|
July 17, 2023
Identifying Biomarkers of Spinal Muscular Atrophy for Further Development
Jacqueline Glascock, Basil T Darras, Thomas O Crawford, et al.
Journal of Neuromuscular Diseases
|
April 5, 2018
Treatment Algorithm for Infants Diagnosed with Spinal Muscular Atrophy through Newborn Screening
Jacqueline Glascock, Jacinda Sampson, Amanda Haidet-Phillips, et al.
Annals of Neurology
|
November 5, 2003
Valproic acid increases SMN levels in spinal muscular atrophy patient cells
Charlotte J Sumner, Thanh N Huynh, Jennifer A Markowitz, et al.
Human Molecular Genetics
|
November 10, 2009
Effects of 2,4-diaminoquinazoline derivatives on SMN expression and phenotype in a mouse model for spinal muscular atrophy
Matthew E R Butchbach, Jasbir Singh, Margrét Thorsteinsdóttir, et al.
Page
of 4