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Biorxiv : the Preprint Server for Biology|January 3, 2024
AAV-mediated interneuron-specific gene replacement for Dravet syndromeJohn K Mich, Jiyun Ryu, Aguan D Wei, et al.
Science Translational Medicine|March 19, 2025
Interneuron-specific dual-AAV SCN1A gene replacement corrects epileptic phenotypes in mouse models of Dravet syndromeJohn K Mich, Jiyun Ryu, Aguan D Wei, et al.
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