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Current Opinion in Molecular Therapeutics
|
September 12, 2002
Gene therapy for the lysosomal storage disorders
Mario A Cabrera-Salazar, Enrico Novelli, John A Barranger
The Journal of Pediatrics
|
July 20, 2005
Radiological evidence of early cerebral microvascular disease in young children with Fabry disease
Mario A Cabrera-Salazar, Erin O'Rourke, Gustavo Charria-Ortiz, et al.
Methods in Molecular Medicine
|
May 4, 2002
Retrovirus-mediated gene transfer to human hematopoietic stem cells
William P Swaney, Enrico M Novelli, Alfred B Bahnson, et al.
Clinica Chimica Acta; International Journal of Clinical Chemistry
|
May 20, 2004
Correlation of surrogate markers of Gaucher disease. Implications for long-term follow up of enzyme replacement therapy
Mario A Cabrera-Salazar, Erin O'Rourke, Nadene Henderson, et al.
American Journal of Hematology
|
October 26, 2005
Guidance on the use of miglustat for treating patients with type 1 Gaucher disease
Neal J Weinreb, John A Barranger, Joel Charrow, et al.
American Journal of Hematology
|
February 4, 2014
Position statement: National Gaucher Foundation Medical Advisory Board, January 7, 2014
John A Barranger, Roscoe O Brady, Gregory A Grabowski, et al.
Journal of Genetic Counseling
|
May 9, 2003
Fabry disease in genetic counseling practice: recommendations of the National Society of Genetic Counselors
Robin L Bennett, Kimberly A Hart, Erin O'Rourke, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy
|
August 6, 2002
Demonstration of feasibility of in vivo gene therapy for Gaucher disease using a chemically induced mouse model
John Marshall, Kerry Anne McEachern, Julie A Cavanagh Kyros, et al.
Molecular Genetics and Metabolism
|
December 17, 2008
Lysosomal Disease Network's "WORLD Symposium 2009". Introduction
Chester B Whitley, John A Barranger, Christine M Eng, et al.
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of 1
Search research articles
Search
Showing results (1-10 of 9) with videos related to
Sort By:
Page
of 1
Current Opinion in Molecular Therapeutics
|
September 12, 2002
Gene therapy for the lysosomal storage disorders
Mario A Cabrera-Salazar, Enrico Novelli, John A Barranger
The Journal of Pediatrics
|
July 20, 2005
Radiological evidence of early cerebral microvascular disease in young children with Fabry disease
Mario A Cabrera-Salazar, Erin O'Rourke, Gustavo Charria-Ortiz, et al.
Methods in Molecular Medicine
|
May 4, 2002
Retrovirus-mediated gene transfer to human hematopoietic stem cells
William P Swaney, Enrico M Novelli, Alfred B Bahnson, et al.
Clinica Chimica Acta; International Journal of Clinical Chemistry
|
May 20, 2004
Correlation of surrogate markers of Gaucher disease. Implications for long-term follow up of enzyme replacement therapy
Mario A Cabrera-Salazar, Erin O'Rourke, Nadene Henderson, et al.
American Journal of Hematology
|
October 26, 2005
Guidance on the use of miglustat for treating patients with type 1 Gaucher disease
Neal J Weinreb, John A Barranger, Joel Charrow, et al.
American Journal of Hematology
|
February 4, 2014
Position statement: National Gaucher Foundation Medical Advisory Board, January 7, 2014
John A Barranger, Roscoe O Brady, Gregory A Grabowski, et al.
Journal of Genetic Counseling
|
May 9, 2003
Fabry disease in genetic counseling practice: recommendations of the National Society of Genetic Counselors
Robin L Bennett, Kimberly A Hart, Erin O'Rourke, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy
|
August 6, 2002
Demonstration of feasibility of in vivo gene therapy for Gaucher disease using a chemically induced mouse model
John Marshall, Kerry Anne McEachern, Julie A Cavanagh Kyros, et al.
Molecular Genetics and Metabolism
|
December 17, 2008
Lysosomal Disease Network's "WORLD Symposium 2009". Introduction
Chester B Whitley, John A Barranger, Christine M Eng, et al.
Page
of 1