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Molecular Metabolism|February 12, 2024
Treatment of infantile-onset Pompe disease in a rat model with muscle-directed AAV gene therapySergio Muñoz, Joan Bertolin, Veronica Jimenez, et al.
Nature Communications|June 22, 2023
Striated muscle-specific base editing enables correction of mutations causing dilated cardiomyopathyMarkus Grosch, Laura Schraft, Adrian Chan, et al.
Communications Biology|July 15, 2024
Influence of AAV vector tropism on long-term expression and Fc-γ receptor binding of an antibody targeting SARS-CoV-2Jannik T Wagner, Sandra M Müller-Schmucker, Wenjun Wang, et al.
Cell Reports|August 18, 2021
The angiopoietin-Tie2 pathway regulates Purkinje cell dendritic morphogenesis in a cell-autonomous mannerRobert Luck, Andromachi Karakatsani, Bhavin Shah, et al.
Frontiers in Molecular Neuroscience|January 31, 2018
Regulation of Adult CNS Axonal Regeneration by the Post-transcriptional Regulator Cpeb1Wilson Pak-Kin Lou, Alvaro Mateos, Marta Koch, et al.
Nucleic Acids Research|September 20, 2013
Robust RNAi enhancement via human Argonaute-2 overexpression from plasmids, viral vectors and cell linesKathleen Börner, Dominik Niopek, Gabriella Cotugno, et al.
Advanced Science (Weinheim, Baden-Wurttemberg, Germany)|October 28, 2025
DKK3 Initially Preserves Acinar Integrity Through MEK-Fos Signaling, but Later Switches to an Oncogenic Role in Pancreatic CancerDharini Srinivasan, Elodie Roger, Lukas Perkhofer, et al.
Nature Communications|November 25, 2021
Cas9-specific immune responses compromise local and systemic AAV CRISPR therapy in multiple dystrophic canine modelsChady H Hakim, Sandeep R P Kumar, Dennis O Pérez-López, et al.
Viruses|August 14, 2020
SARS-CoV-2 RNA Extraction Using Magnetic Beads for Rapid Large-Scale Testing by RT-qPCR and RT-LAMPSteffen Klein, Thorsten G Müller, Dina Khalid, et al.
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