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American Journal of Human Genetics
|
October 7, 2004
Mutations in the AHI1 gene, encoding jouberin, cause Joubert syndrome with cortical polymicrogyria
Tracy Dixon-Salazar, Jennifer L Silhavy, Sarah E Marsh, et al.
Journal of Molecular Neuroscience : MN
|
October 4, 2024
Clinical and Molecular Profiles of a Cohort of Egyptian Patients with Collagen VI-Related Dystrophy
Wessam E Sharaf-Eldin, Karima Rafat, Mahmoud Y Issa, et al.
American Journal of Medical Genetics. Part A
|
March 23, 2016
Extending the mutation spectrum for Galloway-Mowat syndrome to include homozygous missense mutations in the WDR73 gene
Rasim O Rosti, Esra Dikoglu, Maha S Zaki, et al.
Annals of Neurology
|
May 1, 2016
PYCR2 Mutations cause a lethal syndrome of microcephaly and failure to thrive
Maha S Zaki, Gifty Bhat, Tipu Sultan, et al.
NPJ Genomic Medicine
|
January 29, 2022
Oligonucleotide correction of an intronic TIMMDC1 variant in cells of patients with severe neurodegenerative disorder
Raman Kumar, Mark A Corbett, Nicholas J C Smith, et al.
Journal of Medical Genetics
|
May 23, 2020
Bi-allelic <i>TTC5</i> variants cause delayed developmental milestones and intellectual disability
Arisha Rasheed, Evren Gumus, Maha Zaki, et al.
BMC Medical Genomics
|
May 15, 2020
Molecular diagnosis in recessive pediatric neurogenetic disease can help reduce disease recurrence in families
Mahmoud Y Issa, Zinayida Chechlacz, Valentina Stanley, et al.
Nature Medicine
|
August 9, 2024
Antisense oligonucleotide therapy in an individual with KIF1A-associated neurological disorder
Alban Ziegler, Joanne Carroll, Jennifer M Bain, et al.
Cell Reports
|
January 15, 2023
Reversibility and developmental neuropathology of linear nevus sebaceous syndrome caused by dysregulation of the RAS pathway
Ye Eun Kim, Yong-Seok Kim, Hee-Eun Lee, et al.
Nature Communications
|
November 12, 2024
A framework for N-of-1 trials of individualized gene-targeted therapies for genetic diseases
Olivia Kim-McManus, Joseph G Gleeson, Laurence Mignon, et al.
Page
of 33
Search research articles
Search
Showing results (131-140 of 325) with videos related to
Sort By:
Page
of 33
American Journal of Human Genetics
|
October 7, 2004
Mutations in the AHI1 gene, encoding jouberin, cause Joubert syndrome with cortical polymicrogyria
Tracy Dixon-Salazar, Jennifer L Silhavy, Sarah E Marsh, et al.
Journal of Molecular Neuroscience : MN
|
October 4, 2024
Clinical and Molecular Profiles of a Cohort of Egyptian Patients with Collagen VI-Related Dystrophy
Wessam E Sharaf-Eldin, Karima Rafat, Mahmoud Y Issa, et al.
American Journal of Medical Genetics. Part A
|
March 23, 2016
Extending the mutation spectrum for Galloway-Mowat syndrome to include homozygous missense mutations in the WDR73 gene
Rasim O Rosti, Esra Dikoglu, Maha S Zaki, et al.
Annals of Neurology
|
May 1, 2016
PYCR2 Mutations cause a lethal syndrome of microcephaly and failure to thrive
Maha S Zaki, Gifty Bhat, Tipu Sultan, et al.
NPJ Genomic Medicine
|
January 29, 2022
Oligonucleotide correction of an intronic TIMMDC1 variant in cells of patients with severe neurodegenerative disorder
Raman Kumar, Mark A Corbett, Nicholas J C Smith, et al.
Journal of Medical Genetics
|
May 23, 2020
Bi-allelic <i>TTC5</i> variants cause delayed developmental milestones and intellectual disability
Arisha Rasheed, Evren Gumus, Maha Zaki, et al.
BMC Medical Genomics
|
May 15, 2020
Molecular diagnosis in recessive pediatric neurogenetic disease can help reduce disease recurrence in families
Mahmoud Y Issa, Zinayida Chechlacz, Valentina Stanley, et al.
Nature Medicine
|
August 9, 2024
Antisense oligonucleotide therapy in an individual with KIF1A-associated neurological disorder
Alban Ziegler, Joanne Carroll, Jennifer M Bain, et al.
Cell Reports
|
January 15, 2023
Reversibility and developmental neuropathology of linear nevus sebaceous syndrome caused by dysregulation of the RAS pathway
Ye Eun Kim, Yong-Seok Kim, Hee-Eun Lee, et al.
Nature Communications
|
November 12, 2024
A framework for N-of-1 trials of individualized gene-targeted therapies for genetic diseases
Olivia Kim-McManus, Joseph G Gleeson, Laurence Mignon, et al.
Page
of 33