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Orphanet Journal of Rare Diseases
|
June 21, 2017
Do investors value the FDA orphan drug designation?
Kathleen L Miller
Orphanet Journal of Rare Diseases
|
October 24, 2018
Investigating the landscape of US orphan product approvals
Kathleen L Miller, Michael Lanthier
Health Affairs (Project Hope)
|
March 9, 2016
Trends In Orphan New Molecular Entities, 1983-2014: Half Were First In Class, And Rare Cancers Were The Most Frequent Target
Kathleen L Miller, Michael Lanthier
Value in Health : the Journal of the International Society for Pharmacoeconomics and Outcomes Research
|
February 27, 2017
Value Assessment in the Regulatory Context
Kathleen L Miller, Janet Woodcock
Nature Reviews. Drug Discovery
|
January 31, 2015
Regulatory watch: Innovation in biologic new molecular entities: 1986-2014
Kathleen L Miller, Michael Lanthier
Health Affairs (Project Hope)
|
January 8, 2024
Orphan Drug Label Expansions: Analysis Of Subsequent Rare And Common Indication Approvals
Kathleen L Miller, Michael Lanthier
Orphanet Journal of Rare Diseases
|
June 23, 2023
A comprehensive study of the rare diseases and conditions targeted by orphan drug designations and approvals over the forty years of the Orphan Drug Act
Lewis J Fermaglich, Kathleen L Miller
Contemporary Clinical Trials
|
April 17, 2023
The effect of the COVID-19 pandemic on US Food and Drug Administration-funded clinical trials and natural history studies for rare diseases
Kathleen L Miller, Katherine I Miller Needleman
Nature Reviews. Drug Discovery
|
September 4, 2019
Transition probabilities for clinical trials: investigating individual diseases
Kathleen L Miller, Dina Rabinovitz, Kirk W Kerr
Orphanet Journal of Rare Diseases
|
June 10, 2021
Using four decades of FDA orphan drug designations to describe trends in rare disease drug development: substantial growth seen in development of drugs for rare oncologic, neurologic, and pediatric-onset diseases
Kathleen L Miller, Lewis J Fermaglich, Janet Maynard
Page
of 4
Search research articles
Search
Showing results (1-10 of 31) with videos related to
Sort By:
Page
of 4
Orphanet Journal of Rare Diseases
|
June 21, 2017
Do investors value the FDA orphan drug designation?
Kathleen L Miller
Orphanet Journal of Rare Diseases
|
October 24, 2018
Investigating the landscape of US orphan product approvals
Kathleen L Miller, Michael Lanthier
Health Affairs (Project Hope)
|
March 9, 2016
Trends In Orphan New Molecular Entities, 1983-2014: Half Were First In Class, And Rare Cancers Were The Most Frequent Target
Kathleen L Miller, Michael Lanthier
Value in Health : the Journal of the International Society for Pharmacoeconomics and Outcomes Research
|
February 27, 2017
Value Assessment in the Regulatory Context
Kathleen L Miller, Janet Woodcock
Nature Reviews. Drug Discovery
|
January 31, 2015
Regulatory watch: Innovation in biologic new molecular entities: 1986-2014
Kathleen L Miller, Michael Lanthier
Health Affairs (Project Hope)
|
January 8, 2024
Orphan Drug Label Expansions: Analysis Of Subsequent Rare And Common Indication Approvals
Kathleen L Miller, Michael Lanthier
Orphanet Journal of Rare Diseases
|
June 23, 2023
A comprehensive study of the rare diseases and conditions targeted by orphan drug designations and approvals over the forty years of the Orphan Drug Act
Lewis J Fermaglich, Kathleen L Miller
Contemporary Clinical Trials
|
April 17, 2023
The effect of the COVID-19 pandemic on US Food and Drug Administration-funded clinical trials and natural history studies for rare diseases
Kathleen L Miller, Katherine I Miller Needleman
Nature Reviews. Drug Discovery
|
September 4, 2019
Transition probabilities for clinical trials: investigating individual diseases
Kathleen L Miller, Dina Rabinovitz, Kirk W Kerr
Orphanet Journal of Rare Diseases
|
June 10, 2021
Using four decades of FDA orphan drug designations to describe trends in rare disease drug development: substantial growth seen in development of drugs for rare oncologic, neurologic, and pediatric-onset diseases
Kathleen L Miller, Lewis J Fermaglich, Janet Maynard
Page
of 4