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Aging Cell
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December 14, 2020
Directly converted astrocytes retain the ageing features of the donor fibroblasts and elucidate the astrocytic contribution to human CNS health and disease
Noemi Gatto, Cleide Dos Santos Souza, Allan C Shaw, et al.
Cell Reports Methods
|
July 5, 2022
Optimization and validation of CAR transduction into human primary NK cells using CRISPR and AAV
Meisam Naeimi Kararoudi, Shibi Likhite, Ezgi Elmas, et al.
Molecular Therapy. Nucleic Acids
|
September 10, 2018
Translating SOD1 Gene Silencing toward the Clinic: A Highly Efficacious, Off-Target-free, and Biomarker-Supported Strategy for fALS
Tommaso Iannitti, Joseph M Scarrott, Shibi Likhite, et al.
Frontiers in Genetics
|
April 10, 2023
Early postnatal administration of an AAV9 gene therapy is safe and efficacious in CLN3 disease
Tyler B Johnson, Jon J Brudvig, Shibi Likhite, et al.
The EMBO Journal
|
June 24, 2016
The C9orf72 protein interacts with Rab1a and the ULK1 complex to regulate initiation of autophagy
Christopher P Webster, Emma F Smith, Claudia S Bauer, et al.
Nature Biotechnology
|
August 12, 2011
Astrocytes from familial and sporadic ALS patients are toxic to motor neurons
Amanda M Haidet-Phillips, Mark E Hester, Carlos J Miranda, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy
|
July 24, 2019
Gene Therapy Corrects Brain and Behavioral Pathologies in CLN6-Batten Disease
Jacob T Cain, Shibi Likhite, Katherine A White, et al.
JCI Insight
|
November 16, 2018
AAV-mediated follistatin gene therapy improves functional outcomes in the TIC-DUX4 mouse model of FSHD
Carlee R Giesige, Lindsay M Wallace, Kristin N Heller, et al.
Acta Neuropathologica
|
September 19, 2022
PolyGA targets the ER stress-adaptive response by impairing GRP75 function at the MAM in C9ORF72-ALS/FTD
Federica Pilotto, Alexander Schmitz, Niran Maharjan, et al.
The New England Journal of Medicine
|
November 2, 2017
Single-Dose Gene-Replacement Therapy for Spinal Muscular Atrophy
Jerry R Mendell, Samiah Al-Zaidy, Richard Shell, et al.
Page
of 7
Search research articles
Search
Showing results (51-60 of 61) with videos related to
Sort By:
Page
of 7
Aging Cell
|
December 14, 2020
Directly converted astrocytes retain the ageing features of the donor fibroblasts and elucidate the astrocytic contribution to human CNS health and disease
Noemi Gatto, Cleide Dos Santos Souza, Allan C Shaw, et al.
Cell Reports Methods
|
July 5, 2022
Optimization and validation of CAR transduction into human primary NK cells using CRISPR and AAV
Meisam Naeimi Kararoudi, Shibi Likhite, Ezgi Elmas, et al.
Molecular Therapy. Nucleic Acids
|
September 10, 2018
Translating SOD1 Gene Silencing toward the Clinic: A Highly Efficacious, Off-Target-free, and Biomarker-Supported Strategy for fALS
Tommaso Iannitti, Joseph M Scarrott, Shibi Likhite, et al.
Frontiers in Genetics
|
April 10, 2023
Early postnatal administration of an AAV9 gene therapy is safe and efficacious in CLN3 disease
Tyler B Johnson, Jon J Brudvig, Shibi Likhite, et al.
The EMBO Journal
|
June 24, 2016
The C9orf72 protein interacts with Rab1a and the ULK1 complex to regulate initiation of autophagy
Christopher P Webster, Emma F Smith, Claudia S Bauer, et al.
Nature Biotechnology
|
August 12, 2011
Astrocytes from familial and sporadic ALS patients are toxic to motor neurons
Amanda M Haidet-Phillips, Mark E Hester, Carlos J Miranda, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy
|
July 24, 2019
Gene Therapy Corrects Brain and Behavioral Pathologies in CLN6-Batten Disease
Jacob T Cain, Shibi Likhite, Katherine A White, et al.
JCI Insight
|
November 16, 2018
AAV-mediated follistatin gene therapy improves functional outcomes in the TIC-DUX4 mouse model of FSHD
Carlee R Giesige, Lindsay M Wallace, Kristin N Heller, et al.
Acta Neuropathologica
|
September 19, 2022
PolyGA targets the ER stress-adaptive response by impairing GRP75 function at the MAM in C9ORF72-ALS/FTD
Federica Pilotto, Alexander Schmitz, Niran Maharjan, et al.
The New England Journal of Medicine
|
November 2, 2017
Single-Dose Gene-Replacement Therapy for Spinal Muscular Atrophy
Jerry R Mendell, Samiah Al-Zaidy, Richard Shell, et al.
Page
of 7