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Blood|May 10, 2011
Prognostic significance of additional cytogenetic aberrations in 733 de novo pediatric 11q23/MLL-rearranged AML patients: results of an international studyEva A Coenen, Susana C Raimondi, Jochen Harbott, et al.Blood|June 17, 2009
Novel prognostic subgroups in childhood 11q23/MLL-rearranged acute myeloid leukemia: results of an international retrospective studyBrian V Balgobind, Susana C Raimondi, Jochen Harbott, et al.The Journal of Clinical Investigation|March 28, 2017
Clinical efficacy of gene-modified stem cells in adenosine deaminase-deficient immunodeficiencyKit L Shaw, Elizabeth Garabedian, Suparna Mishra, et al.Clinical Cancer Research : an Official Journal of the American Association for Cancer Research|November 10, 2018
IND-Enabling Studies for a Clinical Trial to Genetically Program a Persistent Cancer-Targeted Immune SystemCristina Puig-Saus, Giulia Parisi, Angel Garcia-Diaz, et al.The New England Journal of Medicine|May 11, 2021
Autologous Ex Vivo Lentiviral Gene Therapy for Adenosine Deaminase DeficiencyDonald B Kohn, Claire Booth, Kit L Shaw, et al.Cell|August 7, 2012
Identification of regulators of polyploidization presents therapeutic targets for treatment of AMKLQiang Wen, Benjamin Goldenson, Serena J Silver, et al.Pageof 15