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Science Translational Medicine
|
August 26, 2011
A tale of two SCIDs
Kit L Shaw, Donald B Kohn
Journal of Virology
|
January 29, 2003
Foamy virus envelope glycoprotein is sufficient for particle budding and release
Kit L Shaw, Dirk Lindemann, Mark J Mulligan, et al.
Biology of Blood and Marrow Transplantation : Journal of the American Society for Blood and Marrow Transplantation
|
July 13, 2020
Busulfan Pharmacokinetics in Adenosine Deaminase-Deficient Severe Combined Immunodeficiency Gene Therapy
Kathryn L Bradford, Siyu Liu, Maja Krajinovic, et al.
Biorxiv : the Preprint Server for Biology
|
August 30, 2024
Scalable assessment of genome editing off-targets associated with genetic variants
Jiecong Lin, My Anh Nguyen, Linda Y Lin, et al.
Nature Communications
|
March 4, 2025
Cultivated autologous limbal epithelial cell (CALEC) transplantation for limbal tem cell deficiency: a phase I/II clinical trial of the first xenobiotic-free, serum-free, antibiotic-free manufacturing protocol developed in the US
Ula V Jurkunas, Aaron R Kaufman, Jia Yin, et al.
Science Advances
|
August 18, 2023
Cultivated autologous limbal epithelial cell (CALEC) transplantation: Development of manufacturing process and clinical evaluation of feasibility and safety
Ula V Jurkunas, Jia Yin, Lynette K Johns, et al.
Blood
|
June 3, 2026
Long-term stability of posttranscriptional genetic silencing of BCL11A using a shmiR vector in Sickle Cell Disease
Erica B Esrick, Leslie Lehmann, Amy Federico, et al.
Blood
|
May 11, 2021
Long-term outcomes after gene therapy for adenosine deaminase severe combined immune deficiency
Bryanna Reinhardt, Omar Habib, Kit L Shaw, et al.
The Journal of Clinical Investigation
|
March 28, 2017
Clinical efficacy of gene-modified stem cells in adenosine deaminase-deficient immunodeficiency
Kit L Shaw, Elizabeth Garabedian, Suparna Mishra, et al.
Blood
|
September 13, 2012
Gene therapy for adenosine deaminase-deficient severe combined immune deficiency: clinical comparison of retroviral vectors and treatment plans
Fabio Candotti, Kit L Shaw, Linda Muul, et al.
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of 2
Search research articles
Search
Showing results (1-10 of 13) with videos related to
Sort By:
Page
of 2
Science Translational Medicine
|
August 26, 2011
A tale of two SCIDs
Kit L Shaw, Donald B Kohn
Journal of Virology
|
January 29, 2003
Foamy virus envelope glycoprotein is sufficient for particle budding and release
Kit L Shaw, Dirk Lindemann, Mark J Mulligan, et al.
Biology of Blood and Marrow Transplantation : Journal of the American Society for Blood and Marrow Transplantation
|
July 13, 2020
Busulfan Pharmacokinetics in Adenosine Deaminase-Deficient Severe Combined Immunodeficiency Gene Therapy
Kathryn L Bradford, Siyu Liu, Maja Krajinovic, et al.
Biorxiv : the Preprint Server for Biology
|
August 30, 2024
Scalable assessment of genome editing off-targets associated with genetic variants
Jiecong Lin, My Anh Nguyen, Linda Y Lin, et al.
Nature Communications
|
March 4, 2025
Cultivated autologous limbal epithelial cell (CALEC) transplantation for limbal tem cell deficiency: a phase I/II clinical trial of the first xenobiotic-free, serum-free, antibiotic-free manufacturing protocol developed in the US
Ula V Jurkunas, Aaron R Kaufman, Jia Yin, et al.
Science Advances
|
August 18, 2023
Cultivated autologous limbal epithelial cell (CALEC) transplantation: Development of manufacturing process and clinical evaluation of feasibility and safety
Ula V Jurkunas, Jia Yin, Lynette K Johns, et al.
Blood
|
June 3, 2026
Long-term stability of posttranscriptional genetic silencing of BCL11A using a shmiR vector in Sickle Cell Disease
Erica B Esrick, Leslie Lehmann, Amy Federico, et al.
Blood
|
May 11, 2021
Long-term outcomes after gene therapy for adenosine deaminase severe combined immune deficiency
Bryanna Reinhardt, Omar Habib, Kit L Shaw, et al.
The Journal of Clinical Investigation
|
March 28, 2017
Clinical efficacy of gene-modified stem cells in adenosine deaminase-deficient immunodeficiency
Kit L Shaw, Elizabeth Garabedian, Suparna Mishra, et al.
Blood
|
September 13, 2012
Gene therapy for adenosine deaminase-deficient severe combined immune deficiency: clinical comparison of retroviral vectors and treatment plans
Fabio Candotti, Kit L Shaw, Linda Muul, et al.
Page
of 2