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American Journal of Hematology
|
October 8, 2009
Production of beta-globin and adult hemoglobin following G418 treatment of erythroid precursor cells from homozygous beta(0)39 thalassemia patients
Francesca Salvatori, Giulia Breveglieri, Cristina Zuccato, et al.
Blood
|
June 2, 2019
Lack of <i>Gdf11</i> does not improve anemia or prevent the activity of RAP-536 in a mouse model of β-thalassemia
Amaliris Guerra, Paraskevi Rea Oikonomidou, Sayantani Sinha, et al.
Haematologica
|
May 28, 2021
Inclusion of a short hairpin RNA targeting <i>BCL11A</i> into a β-globin expressing vector allows concurrent synthesis of curative adult and fetal hemoglobin
Silvia Pires Lourenco, Danuta Jarocha, Valentina Ghiaccio, et al.
Journal of Translational Medicine
|
September 4, 2016
A validated cellular biobank for β-thalassemia
Lucia Carmela Cosenza, Laura Breda, Giulia Breveglieri, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy
|
March 15, 2025
CD47 peptide-cloaked lipid nanoparticles promote cell-specific mRNA delivery
Tyler Ellis Papp, Jianhao Zeng, Hamna Shahnawaz, et al.
Blood
|
December 10, 2024
An erythroid-specific lentiviral vector improves anemia and iron metabolism in a new model of XLSA
Carlo Castruccio Castracani, Laura Breda, Tyler E Papp, et al.
Biomed Research International
|
June 23, 2015
Generation and Characterization of a Transgenic Mouse Carrying a Functional Human β -Globin Gene with the IVSI-6 Thalassemia Mutation
Giulia Breveglieri, Irene Mancini, Nicoletta Bianchi, et al.
Plos One
|
April 6, 2012
Therapeutic hemoglobin levels after gene transfer in β-thalassemia mice and in hematopoietic cells of β-thalassemia and sickle cells disease patients
Laura Breda, Carla Casu, Sara Gardenghi, et al.
Science (New York, N.Y.)
|
July 27, 2023
In vivo hematopoietic stem cell modification by mRNA delivery
Laura Breda, Tyler E Papp, Michael P Triebwasser, et al.
Biorxiv : the Preprint Server for Biology
|
April 1, 2024
Effective Gene Therapy for Metachromatic Leukodystrophy Achieved with Minimal Lentiviral Genomic Integrations
Lucas Tricoli, Sunetra Sase, Julia Hacker, et al.
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Search research articles
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Showing results (31-40 of 48) with videos related to
Sort By:
Page
of 5
American Journal of Hematology
|
October 8, 2009
Production of beta-globin and adult hemoglobin following G418 treatment of erythroid precursor cells from homozygous beta(0)39 thalassemia patients
Francesca Salvatori, Giulia Breveglieri, Cristina Zuccato, et al.
Blood
|
June 2, 2019
Lack of <i>Gdf11</i> does not improve anemia or prevent the activity of RAP-536 in a mouse model of β-thalassemia
Amaliris Guerra, Paraskevi Rea Oikonomidou, Sayantani Sinha, et al.
Haematologica
|
May 28, 2021
Inclusion of a short hairpin RNA targeting <i>BCL11A</i> into a β-globin expressing vector allows concurrent synthesis of curative adult and fetal hemoglobin
Silvia Pires Lourenco, Danuta Jarocha, Valentina Ghiaccio, et al.
Journal of Translational Medicine
|
September 4, 2016
A validated cellular biobank for β-thalassemia
Lucia Carmela Cosenza, Laura Breda, Giulia Breveglieri, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy
|
March 15, 2025
CD47 peptide-cloaked lipid nanoparticles promote cell-specific mRNA delivery
Tyler Ellis Papp, Jianhao Zeng, Hamna Shahnawaz, et al.
Blood
|
December 10, 2024
An erythroid-specific lentiviral vector improves anemia and iron metabolism in a new model of XLSA
Carlo Castruccio Castracani, Laura Breda, Tyler E Papp, et al.
Biomed Research International
|
June 23, 2015
Generation and Characterization of a Transgenic Mouse Carrying a Functional Human β -Globin Gene with the IVSI-6 Thalassemia Mutation
Giulia Breveglieri, Irene Mancini, Nicoletta Bianchi, et al.
Plos One
|
April 6, 2012
Therapeutic hemoglobin levels after gene transfer in β-thalassemia mice and in hematopoietic cells of β-thalassemia and sickle cells disease patients
Laura Breda, Carla Casu, Sara Gardenghi, et al.
Science (New York, N.Y.)
|
July 27, 2023
In vivo hematopoietic stem cell modification by mRNA delivery
Laura Breda, Tyler E Papp, Michael P Triebwasser, et al.
Biorxiv : the Preprint Server for Biology
|
April 1, 2024
Effective Gene Therapy for Metachromatic Leukodystrophy Achieved with Minimal Lentiviral Genomic Integrations
Lucas Tricoli, Sunetra Sase, Julia Hacker, et al.
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