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Muscle & Nerve
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August 27, 2014
Correlation between quantitative whole-body muscle magnetic resonance imaging and clinical muscle weakness in Pompe disease
Jeffrey J Horvath, Stephanie L Austin, Laura E Case, et al.
Molecular Genetics and Metabolism Reports
|
September 24, 2024
Optimizing clinical outcomes: The journey of twins with CRIM-negative infantile-onset Pompe disease on high-dose enzyme replacement therapy and immunomodulation
Angie H Fares, Ankit K Desai, Laura E Case, et al.
Genetics in Medicine : Official Journal of the American College of Medical Genetics
|
January 7, 2020
Higher dosing of alglucosidase alfa improves outcomes in children with Pompe disease: a clinical study and review of the literature
Aleena A Khan, Laura E Case, Mrudu Herbert, et al.
Molecular Genetics and Metabolism
|
April 5, 2026
Early enzyme replacement therapy in late-onset Pompe disease diagnosed by newborn screening
Laura E Case, Erin Huggins, Harrison N Jones, et al.
Molecular Genetics and Metabolism
|
February 11, 2017
The emerging phenotype of late-onset Pompe disease: A systematic literature review
Justin Chan, Ankit K Desai, Zoheb B Kazi, et al.
Dysphagia
|
September 19, 2009
Oropharyngeal dysphagia in infants and children with infantile Pompe disease
Harrison N Jones, Carolyn W Muller, Min Lin, et al.
Cold Spring Harbor Molecular Case Studies
|
May 6, 2016
Sustained therapeutic response to riboflavin in a child with a progressive neurological condition, diagnosed by whole-exome sequencing
Vandana Shashi, Slavé Petrovski, Kelly Schoch, et al.
Molecular Genetics and Metabolism
|
December 17, 2019
Improved muscle function in a phase I/II clinical trial of albuterol in Pompe disease
Dwight D Koeberl, Laura E Case, Ankit Desai, et al.
Molecular Genetics and Metabolism
|
September 28, 2017
Insight into the phenotype of infants with Pompe disease identified by newborn screening with the common c.-32-13T>G "late-onset" GAA variant
Mugdha V Rairikar, Laura E Case, Lauren A Bailey, et al.
Journal of Pediatric Rehabilitation Medicine
|
September 28, 2014
Effects of respiratory muscle training (RMT) in children with infantile-onset Pompe disease and respiratory muscle weakness
Harrison N Jones, Kelly D Crisp, Tronda Moss, et al.
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of 6
Search research articles
Search
Showing results (31-40 of 57) with videos related to
Sort By:
Page
of 6
Muscle & Nerve
|
August 27, 2014
Correlation between quantitative whole-body muscle magnetic resonance imaging and clinical muscle weakness in Pompe disease
Jeffrey J Horvath, Stephanie L Austin, Laura E Case, et al.
Molecular Genetics and Metabolism Reports
|
September 24, 2024
Optimizing clinical outcomes: The journey of twins with CRIM-negative infantile-onset Pompe disease on high-dose enzyme replacement therapy and immunomodulation
Angie H Fares, Ankit K Desai, Laura E Case, et al.
Genetics in Medicine : Official Journal of the American College of Medical Genetics
|
January 7, 2020
Higher dosing of alglucosidase alfa improves outcomes in children with Pompe disease: a clinical study and review of the literature
Aleena A Khan, Laura E Case, Mrudu Herbert, et al.
Molecular Genetics and Metabolism
|
April 5, 2026
Early enzyme replacement therapy in late-onset Pompe disease diagnosed by newborn screening
Laura E Case, Erin Huggins, Harrison N Jones, et al.
Molecular Genetics and Metabolism
|
February 11, 2017
The emerging phenotype of late-onset Pompe disease: A systematic literature review
Justin Chan, Ankit K Desai, Zoheb B Kazi, et al.
Dysphagia
|
September 19, 2009
Oropharyngeal dysphagia in infants and children with infantile Pompe disease
Harrison N Jones, Carolyn W Muller, Min Lin, et al.
Cold Spring Harbor Molecular Case Studies
|
May 6, 2016
Sustained therapeutic response to riboflavin in a child with a progressive neurological condition, diagnosed by whole-exome sequencing
Vandana Shashi, Slavé Petrovski, Kelly Schoch, et al.
Molecular Genetics and Metabolism
|
December 17, 2019
Improved muscle function in a phase I/II clinical trial of albuterol in Pompe disease
Dwight D Koeberl, Laura E Case, Ankit Desai, et al.
Molecular Genetics and Metabolism
|
September 28, 2017
Insight into the phenotype of infants with Pompe disease identified by newborn screening with the common c.-32-13T>G "late-onset" GAA variant
Mugdha V Rairikar, Laura E Case, Lauren A Bailey, et al.
Journal of Pediatric Rehabilitation Medicine
|
September 28, 2014
Effects of respiratory muscle training (RMT) in children with infantile-onset Pompe disease and respiratory muscle weakness
Harrison N Jones, Kelly D Crisp, Tronda Moss, et al.
Page
of 6