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Pediatric Radiology
|
March 8, 2007
Fractures in children with Pompe disease: a potential long-term complication
Laura E Case, Rabi Hanna, Donald P Frush, et al.
The Lancet. Neurology
|
December 1, 2009
Diagnosis and management of Duchenne muscular dystrophy, part 1: diagnosis, and pharmacological and psychosocial management
Katharine Bushby, Richard Finkel, David J Birnkrant, et al.
The Lancet. Neurology
|
December 1, 2009
Diagnosis and management of Duchenne muscular dystrophy, part 2: implementation of multidisciplinary care
Katharine Bushby, Richard Finkel, David J Birnkrant, et al.
Genetics in Medicine : Official Journal of the American College of Medical Genetics
|
September 27, 2025
Infantile-onset Pompe disease entering adulthood: Insights from 2 decades of enzyme replacement therapy experience
Neha Regmi, Daniel Kenney-Jung, Grace Stafford, et al.
Genetics in Medicine : Official Journal of the American College of Medical Genetics
|
April 28, 2012
The emerging phenotype of long-term survivors with infantile Pompe disease
Sean N Prater, Suhrad G Banugaria, Stephanie M DeArmey, et al.
Molecular Genetics and Metabolism Reports
|
November 25, 2021
A retrospective longitudinal study and comprehensive review of adult patients with glycogen storage disease type III
Ghada Hijazi, Anna Paschall, Sarah P Young, et al.
Neuromuscular Disorders : NMD
|
January 26, 2015
Safety and efficacy of alternative alglucosidase alfa regimens in Pompe disease
Laura E Case, Carl Bjartmar, Claire Morgan, et al.
Pediatric Physical Therapy : the Official Publication of the Section on Pediatrics of the American Physical Therapy Association
|
April 2, 2013
Reliability and validity of the TIMPSI for infants with spinal muscular atrophy type I
Kristin J Krosschell, Jo Anne Maczulski, Charles Scott, et al.
Cold Spring Harbor Molecular Case Studies
|
May 6, 2016
Exome sequencing results in successful riboflavin treatment of a rapidly progressive neurological condition
Slavé Petrovski, Vandana Shashi, Steven Petrou, et al.
Genetics in Medicine : Official Journal of the American College of Medical Genetics
|
January 13, 2012
Successful immune tolerance induction to enzyme replacement therapy in CRIM-negative infantile Pompe disease
Yoav H Messinger, Nancy J Mendelsohn, William Rhead, et al.
Page
of 6
Search research articles
Search
Showing results (41-50 of 57) with videos related to
Sort By:
Page
of 6
Pediatric Radiology
|
March 8, 2007
Fractures in children with Pompe disease: a potential long-term complication
Laura E Case, Rabi Hanna, Donald P Frush, et al.
The Lancet. Neurology
|
December 1, 2009
Diagnosis and management of Duchenne muscular dystrophy, part 1: diagnosis, and pharmacological and psychosocial management
Katharine Bushby, Richard Finkel, David J Birnkrant, et al.
The Lancet. Neurology
|
December 1, 2009
Diagnosis and management of Duchenne muscular dystrophy, part 2: implementation of multidisciplinary care
Katharine Bushby, Richard Finkel, David J Birnkrant, et al.
Genetics in Medicine : Official Journal of the American College of Medical Genetics
|
September 27, 2025
Infantile-onset Pompe disease entering adulthood: Insights from 2 decades of enzyme replacement therapy experience
Neha Regmi, Daniel Kenney-Jung, Grace Stafford, et al.
Genetics in Medicine : Official Journal of the American College of Medical Genetics
|
April 28, 2012
The emerging phenotype of long-term survivors with infantile Pompe disease
Sean N Prater, Suhrad G Banugaria, Stephanie M DeArmey, et al.
Molecular Genetics and Metabolism Reports
|
November 25, 2021
A retrospective longitudinal study and comprehensive review of adult patients with glycogen storage disease type III
Ghada Hijazi, Anna Paschall, Sarah P Young, et al.
Neuromuscular Disorders : NMD
|
January 26, 2015
Safety and efficacy of alternative alglucosidase alfa regimens in Pompe disease
Laura E Case, Carl Bjartmar, Claire Morgan, et al.
Pediatric Physical Therapy : the Official Publication of the Section on Pediatrics of the American Physical Therapy Association
|
April 2, 2013
Reliability and validity of the TIMPSI for infants with spinal muscular atrophy type I
Kristin J Krosschell, Jo Anne Maczulski, Charles Scott, et al.
Cold Spring Harbor Molecular Case Studies
|
May 6, 2016
Exome sequencing results in successful riboflavin treatment of a rapidly progressive neurological condition
Slavé Petrovski, Vandana Shashi, Steven Petrou, et al.
Genetics in Medicine : Official Journal of the American College of Medical Genetics
|
January 13, 2012
Successful immune tolerance induction to enzyme replacement therapy in CRIM-negative infantile Pompe disease
Yoav H Messinger, Nancy J Mendelsohn, William Rhead, et al.
Page
of 6