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Scientific Reports
|
April 15, 2026
Rescuing TP53 from nonsense: novel triazoles for translational readthrough via optimized drug design
Davide Ricci, Michele Menditto, Giulia Culletta, et al.
European Journal of Medicinal Chemistry
|
July 6, 2015
Enhancement of premature stop codon readthrough in the CFTR gene by Ataluren (PTC124) derivatives
Ivana Pibiri, Laura Lentini, Raffaella Melfi, et al.
Molecular Pharmaceutics
|
February 4, 2014
Toward a rationale for the PTC124 (Ataluren) promoted readthrough of premature stop codons: a computational approach and GFP-reporter cell-based assay
Laura Lentini, Raffaella Melfi, Aldo Di Leonardo, et al.
European Journal of Medicinal Chemistry
|
October 3, 2018
Rescuing the CFTR protein function: Introducing 1,3,4-oxadiazoles as translational readthrough inducing drugs
Ivana Pibiri, Laura Lentini, Raffaella Melfi, et al.
BMC Veterinary Research
|
June 20, 2018
Pharmacokinetics of rectal levetiracetam as add-on treatment in dogs affected by cluster seizures or status epilepticus
Giulia Cagnotti, Rosangela Odore, Giulia Gardini, et al.
IUBMB Life
|
May 27, 2025
Advancing Therapeutic Strategies for Nonsense-Related Diseases: From Small Molecules to Nucleic Acid-Based Innovations
Davide Ricci, Ilenia Cruciata, Ignazio Fiduccia, et al.
IUBMB Life
|
June 6, 2025
Nonsense Mutations in Rare and Ultra-Rare Human Disorders: An Overview
Emanuele Vitale, Davide Ricci, Federica Corrao, et al.
ACS Medicinal Chemistry Letters
|
May 22, 2020
Pharmacophore-Based Design of New Chemical Scaffolds as Translational Readthrough-Inducing Drugs (TRIDs)
Marco Tutone, Ivana Pibiri, Riccardo Perriera, et al.
Neurology. Genetics
|
May 1, 2026
Long-Read HiFi Genome Sequencing Resolves Retrotransposon-Mediated Deletions in TANGO2 Deficiency Disorder
Quentin Sabbagh, Felipe Villa Tobón, Zahra Kazemi, et al.
Nutrients
|
February 26, 2022
Preventive Impact of Long-Term Ingestion of Chestnut Honey on Glucose Disorders and Neurodegeneration in Obese Mice
Simona Terzo, Pasquale Calvi, Domenico Nuzzo, et al.
Page
of 5
Search research articles
Search
Showing results (31-40 of 50) with videos related to
Sort By:
Page
of 5
Scientific Reports
|
April 15, 2026
Rescuing TP53 from nonsense: novel triazoles for translational readthrough via optimized drug design
Davide Ricci, Michele Menditto, Giulia Culletta, et al.
European Journal of Medicinal Chemistry
|
July 6, 2015
Enhancement of premature stop codon readthrough in the CFTR gene by Ataluren (PTC124) derivatives
Ivana Pibiri, Laura Lentini, Raffaella Melfi, et al.
Molecular Pharmaceutics
|
February 4, 2014
Toward a rationale for the PTC124 (Ataluren) promoted readthrough of premature stop codons: a computational approach and GFP-reporter cell-based assay
Laura Lentini, Raffaella Melfi, Aldo Di Leonardo, et al.
European Journal of Medicinal Chemistry
|
October 3, 2018
Rescuing the CFTR protein function: Introducing 1,3,4-oxadiazoles as translational readthrough inducing drugs
Ivana Pibiri, Laura Lentini, Raffaella Melfi, et al.
BMC Veterinary Research
|
June 20, 2018
Pharmacokinetics of rectal levetiracetam as add-on treatment in dogs affected by cluster seizures or status epilepticus
Giulia Cagnotti, Rosangela Odore, Giulia Gardini, et al.
IUBMB Life
|
May 27, 2025
Advancing Therapeutic Strategies for Nonsense-Related Diseases: From Small Molecules to Nucleic Acid-Based Innovations
Davide Ricci, Ilenia Cruciata, Ignazio Fiduccia, et al.
IUBMB Life
|
June 6, 2025
Nonsense Mutations in Rare and Ultra-Rare Human Disorders: An Overview
Emanuele Vitale, Davide Ricci, Federica Corrao, et al.
ACS Medicinal Chemistry Letters
|
May 22, 2020
Pharmacophore-Based Design of New Chemical Scaffolds as Translational Readthrough-Inducing Drugs (TRIDs)
Marco Tutone, Ivana Pibiri, Riccardo Perriera, et al.
Neurology. Genetics
|
May 1, 2026
Long-Read HiFi Genome Sequencing Resolves Retrotransposon-Mediated Deletions in TANGO2 Deficiency Disorder
Quentin Sabbagh, Felipe Villa Tobón, Zahra Kazemi, et al.
Nutrients
|
February 26, 2022
Preventive Impact of Long-Term Ingestion of Chestnut Honey on Glucose Disorders and Neurodegeneration in Obese Mice
Simona Terzo, Pasquale Calvi, Domenico Nuzzo, et al.
Page
of 5