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Nature Communications|July 18, 2023
Mislocalization of pathogenic RBM20 variants in dilated cardiomyopathy is caused by loss-of-interaction with Transportin-3Julia Kornienko, Marta Rodríguez-Martínez, Kai Fenzl, et al.Nature Cardiovascular Research|May 4, 2026
CAMK2D causes heart failure in mice with RBM20 cardiomyopathyMaarten M G van den Hoogenhof, Javier Duran, Thiago Britto-Borges, et al.Nature Communications|June 22, 2023
Striated muscle-specific base editing enables correction of mutations causing dilated cardiomyopathyMarkus Grosch, Laura Schraft, Adrian Chan, et al.Pageof 1