Search research articles
Contact Us
Filters
Showing results (1-10 of 11) with videos related to
Page
of 2
Sort By:
Hepatology (Baltimore, Md.)
|
March 4, 2022
mRNA and gene editing: Late breaking therapies in liver diseases
Nerea Zabaleta, Laura Torella, Nicholas D Weber, et al.
FEBS Letters
|
July 30, 2024
Gene editing in liver diseases
Laura Torella, Nerea Santana-Gonzalez, Nerea Zabaleta, et al.
Case Reports in Genetics
|
August 30, 2018
A Rare Case of Severe Congenital RYR1-Associated Myopathy
Nicola Laforgia, Manuela Capozza, Lucrezia De Cosmo, et al.
Plos Pathogens
|
May 13, 2024
Protective role of RIPK1 scaffolding against HDV-induced hepatocyte cell death and the significance of cytokines in mice
Gracián Camps, Sheila Maestro, Laura Torella, et al.
Kidney International Reports
|
February 24, 2025
CKD in Bardet-Biedl Syndrome: Evidence Supporting Multifactorial Etiology
Miriam Zacchia, Floriana Secondulfo, Andrea Melluso, et al.
Frontiers in Cellular and Infection Microbiology
|
July 5, 2022
Differential Trafficking and Expression of PIR Proteins in Acute and Chronic <i>Plasmodium</i> Infections
Maria Giorgalli, Deirdre A Cunningham, Malgorzata Broncel, et al.
Molecular Therapy. Methods & Clinical Development
|
December 9, 2020
<i>In Vitro</i> and <i>In Vivo</i> Genetic Disease Modeling via NHEJ-Precise Deletions Using CRISPR-Cas9
Sergio López-Manzaneda, Isabel Ojeda-Pérez, Nerea Zabaleta, et al.
Nature Communications
|
December 22, 2018
CRISPR/Cas9-mediated glycolate oxidase disruption is an efficacious and safe treatment for primary hyperoxaluria type I
Nerea Zabaleta, Miren Barberia, Cristina Martin-Higueras, et al.
EMBO Molecular Medicine
|
January 5, 2024
Efficient and safe therapeutic use of paired Cas9-nickases for primary hyperoxaluria type 1
Laura Torella, Julia Klermund, Martin Bilbao-Arribas, et al.
Frontiers in Genome Editing
|
November 19, 2025
Proceedings of the second annual meeting of GenE-HumDi (COST Action 21113)
María Ortiz-Bueno, Iris Ramos-Hernández, Luis Algeciras-Jiménez, et al.
Page
of 2
Search research articles
Search
Showing results (1-10 of 11) with videos related to
Sort By:
Page
of 2
Hepatology (Baltimore, Md.)
|
March 4, 2022
mRNA and gene editing: Late breaking therapies in liver diseases
Nerea Zabaleta, Laura Torella, Nicholas D Weber, et al.
FEBS Letters
|
July 30, 2024
Gene editing in liver diseases
Laura Torella, Nerea Santana-Gonzalez, Nerea Zabaleta, et al.
Case Reports in Genetics
|
August 30, 2018
A Rare Case of Severe Congenital RYR1-Associated Myopathy
Nicola Laforgia, Manuela Capozza, Lucrezia De Cosmo, et al.
Plos Pathogens
|
May 13, 2024
Protective role of RIPK1 scaffolding against HDV-induced hepatocyte cell death and the significance of cytokines in mice
Gracián Camps, Sheila Maestro, Laura Torella, et al.
Kidney International Reports
|
February 24, 2025
CKD in Bardet-Biedl Syndrome: Evidence Supporting Multifactorial Etiology
Miriam Zacchia, Floriana Secondulfo, Andrea Melluso, et al.
Frontiers in Cellular and Infection Microbiology
|
July 5, 2022
Differential Trafficking and Expression of PIR Proteins in Acute and Chronic <i>Plasmodium</i> Infections
Maria Giorgalli, Deirdre A Cunningham, Malgorzata Broncel, et al.
Molecular Therapy. Methods & Clinical Development
|
December 9, 2020
<i>In Vitro</i> and <i>In Vivo</i> Genetic Disease Modeling via NHEJ-Precise Deletions Using CRISPR-Cas9
Sergio López-Manzaneda, Isabel Ojeda-Pérez, Nerea Zabaleta, et al.
Nature Communications
|
December 22, 2018
CRISPR/Cas9-mediated glycolate oxidase disruption is an efficacious and safe treatment for primary hyperoxaluria type I
Nerea Zabaleta, Miren Barberia, Cristina Martin-Higueras, et al.
EMBO Molecular Medicine
|
January 5, 2024
Efficient and safe therapeutic use of paired Cas9-nickases for primary hyperoxaluria type 1
Laura Torella, Julia Klermund, Martin Bilbao-Arribas, et al.
Frontiers in Genome Editing
|
November 19, 2025
Proceedings of the second annual meeting of GenE-HumDi (COST Action 21113)
María Ortiz-Bueno, Iris Ramos-Hernández, Luis Algeciras-Jiménez, et al.
Page
of 2