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Journal of Neuromuscular Diseases
|
November 18, 2016
Accurate Dystrophin Quantification in Mouse Tissue; Identification of New and Evaluation of Existing Methods
Margriet Hulsker, Ingrid Verhaart, Laura van Vliet, et al.
Plos Currents
|
July 22, 2014
Generation of embryonic stem cells and mice for duchenne research
Marcel Veltrop, Jos van der Kaa, Jill Claassens, et al.
Molecular Genetics and Metabolism
|
November 11, 2006
Chemical chaperones improve transport and enhance stability of mutant alpha-glucosidases in glycogen storage disease type II
Toshika Okumiya, Marian A Kroos, Laura Van Vliet, et al.
BMC Medical Genetics
|
December 3, 2008
Assessment of the feasibility of exon 45-55 multiexon skipping for Duchenne muscular dystrophy
Laura van Vliet, Christa L de Winter, Judith C T van Deutekom, et al.
Human Mutation
|
April 22, 2008
Update of the Pompe disease mutation database with 107 sequence variants and a format for severity rating
Marian Kroos, Robert J Pomponio, Laura van Vliet, et al.
Plos One
|
March 31, 2018
Influence of full-length dystrophin on brain volumes in mouse models of Duchenne muscular dystrophy
Bauke Kogelman, Artem Khmelinskii, Ingrid Verhaart, et al.
Molecular Genetics and Metabolism
|
July 15, 2023
Glycoprotein non-metastatic protein B (GPNMB) plasma values in patients with chronic visceral acid sphingomyelinase deficiency
Eline C B Eskes, Martijn J C van der Lienden, Barbara Sjouke, et al.
Plos One
|
February 22, 2018
A dystrophic Duchenne mouse model for testing human antisense oligonucleotides
Marcel Veltrop, Laura van Vliet, Margriet Hulsker, et al.
European Journal of Human Genetics : EJHG
|
February 28, 2008
p.[G576S; E689K]: pathogenic combination or polymorphism in Pompe disease?
Marian A Kroos, Reinier A Mullaart, Laura Van Vliet, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy
|
September 25, 2008
Guidelines for antisense oligonucleotide design and insight into splice-modulating mechanisms
Annemieke Aartsma-Rus, Laura van Vliet, Marscha Hirschi, et al.
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of 2
Search research articles
Search
Showing results (1-10 of 13) with videos related to
Sort By:
Page
of 2
Journal of Neuromuscular Diseases
|
November 18, 2016
Accurate Dystrophin Quantification in Mouse Tissue; Identification of New and Evaluation of Existing Methods
Margriet Hulsker, Ingrid Verhaart, Laura van Vliet, et al.
Plos Currents
|
July 22, 2014
Generation of embryonic stem cells and mice for duchenne research
Marcel Veltrop, Jos van der Kaa, Jill Claassens, et al.
Molecular Genetics and Metabolism
|
November 11, 2006
Chemical chaperones improve transport and enhance stability of mutant alpha-glucosidases in glycogen storage disease type II
Toshika Okumiya, Marian A Kroos, Laura Van Vliet, et al.
BMC Medical Genetics
|
December 3, 2008
Assessment of the feasibility of exon 45-55 multiexon skipping for Duchenne muscular dystrophy
Laura van Vliet, Christa L de Winter, Judith C T van Deutekom, et al.
Human Mutation
|
April 22, 2008
Update of the Pompe disease mutation database with 107 sequence variants and a format for severity rating
Marian Kroos, Robert J Pomponio, Laura van Vliet, et al.
Plos One
|
March 31, 2018
Influence of full-length dystrophin on brain volumes in mouse models of Duchenne muscular dystrophy
Bauke Kogelman, Artem Khmelinskii, Ingrid Verhaart, et al.
Molecular Genetics and Metabolism
|
July 15, 2023
Glycoprotein non-metastatic protein B (GPNMB) plasma values in patients with chronic visceral acid sphingomyelinase deficiency
Eline C B Eskes, Martijn J C van der Lienden, Barbara Sjouke, et al.
Plos One
|
February 22, 2018
A dystrophic Duchenne mouse model for testing human antisense oligonucleotides
Marcel Veltrop, Laura van Vliet, Margriet Hulsker, et al.
European Journal of Human Genetics : EJHG
|
February 28, 2008
p.[G576S; E689K]: pathogenic combination or polymorphism in Pompe disease?
Marian A Kroos, Reinier A Mullaart, Laura Van Vliet, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy
|
September 25, 2008
Guidelines for antisense oligonucleotide design and insight into splice-modulating mechanisms
Annemieke Aartsma-Rus, Laura van Vliet, Marscha Hirschi, et al.
Page
of 2