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Developmental Biology|August 26, 2004
Zebrafish topped is required for ventral motor axon guidanceLouise R Rodino-Klapac, Christine E BeattieCell Research|March 2, 2016
Duchenne muscular dystrophy: CRISPR/Cas9 treatmentJerry R Mendell, Louise R Rodino-KlapacExpert Opinion on Emerging Drugs|May 29, 2012
Emerging drugs for Duchenne muscular dystrophyVinod Malik, Louise R Rodino-Klapac, Jerry R MendellJournal of Child Neurology|May 26, 2010
Molecular therapeutic strategies targeting Duchenne muscular dystrophyJerry R Mendell, Louise R Rodino-Klapac, Vinod MalikCurrent Neurology and Neuroscience Reports|January 19, 2013
Update on the treatment of Duchenne muscular dystrophyLouise R Rodino-Klapac, Jerry R Mendell, Zarife SahenkJournal of Neuromuscular Diseases|March 29, 2021
Evaluation of the Lipid-binding Properties of Recombinant Dystrophin Spectrin-like Repeat Domains R1-3Grace Cooper-Olson, Louise R Rodino-Klapac, Rachael A PotterTherapeutic Advances in Neurological Disorders|December 24, 2010
Aminoglycoside-induced mutation suppression (stop codon readthrough) as a therapeutic strategy for Duchenne muscular dystrophyVinod Malik, Louise R Rodino-Klapac, Laurence Viollet, et al.CPT: Pharmacometrics & Systems Pharmacology|February 26, 2025
A Population Pharmacokinetic Model to Inform Extension of the Eteplirsen Dosing Regimen Across the Broad DMD PopulationYogesh Patel, Larry Orogun, Nicole Yocum, et al.Developmental Biology|December 9, 2008
Semaphorin 5A is a bifunctional axon guidance cue for axial motoneurons in vivoJona D Hilario, Louise R Rodino-Klapac, Chunping Wang, et al.Methods in Molecular Biology (Clifton, N.J.)|January 4, 2011
AAV-mediated gene therapy to the isolated limb in rhesus macaquesLouise R Rodino-Klapac, Chrystal L Montgomery, Jerry R Mendell, et al.Pageof 7