Jove
Visualize
Contact Us
JoVE
x logofacebook logolinkedin logoyoutube logo
ABOUT JoVE
OverviewLeadershipBlogJoVE Help Center
AUTHORS
Publishing ProcessEditorial BoardScope & PoliciesPeer ReviewFAQSubmit
LIBRARIANS
TestimonialsSubscriptionsAccessResourcesLibrary Advisory BoardFAQ
RESEARCH
JoVE JournalMethods CollectionsJoVE Encyclopedia of ExperimentsArchive
EDUCATION
JoVE CoreJoVE BusinessJoVE Science EducationJoVE Lab ManualFaculty Resource CenterFaculty Site
Terms & Conditions of Use
Privacy Policy
Policies

Filters

Lutz Mueller

Showing results (21-30 of 27) with videos related to

Pageof 3
Sort By:
You have reached the last page of results.This site can display upto 27 results.
Pharmacology Research & Perspectives|December 7, 2018
Risdiplam distributes and increases SMN protein in both the central nervous system and peripheral organsAgnès Poirier, Marla Weetall, Katja Heinig, et al.
Drug Metabolism and Disposition: the Biological Fate of Chemicals|October 8, 2021
Addressing Today's Absorption, Distribution, Metabolism, and Excretion (ADME) Challenges in the Translation of In Vitro ADME Characteristics to Humans: A Case Study of the <i>SMN2</i> mRNA Splicing Modifier RisdiplamStephen Fowler, Andreas Brink, Yumi Cleary, et al.
Medrxiv : the Preprint Server for Health Sciences|January 20, 2021
Enisamium is an inhibitor of the SARS-CoV-2 RNA polymerase and shows improvement of recovery in COVID-19 patients in an interim analysis of a clinical trialOlha Holubovska, Denisa Bojkova, Stefano Elli, et al.
Annals of Clinical and Translational Neurology|November 24, 2020
Risdiplam treatment has not led to retinal toxicity in patients with spinal muscular atrophyRobert C Sergott, Giulia M Amorelli, Giovanni Baranello, et al.
Nucleic Acid Therapeutics|May 30, 2025
Developmental and Reproductive Toxicity Testing Strategies for Oligonucleotides: A Workshop ProceedingsBethany R Hannas, Sara M Bender, Eileen Blasi, et al.
Journal of Medicinal Chemistry|June 15, 2016
Specific Correction of Alternative Survival Motor Neuron 2 Splicing by Small Molecules: Discovery of a Potential Novel Medicine To Treat Spinal Muscular AtrophyHasane Ratni, Gary M Karp, Marla Weetall, et al.
Journal of Medicinal Chemistry|July 26, 2018
Discovery of Risdiplam, a Selective Survival of Motor Neuron-2 ( SMN2) Gene Splicing Modifier for the Treatment of Spinal Muscular Atrophy (SMA)Hasane Ratni, Martin Ebeling, John Baird, et al.
Pageof 3

Showing results (21-30 of 27) with videos related to

Sort By:
Pageof 3
You have reached the last page of results.This site can display upto 27 results.
Pharmacology Research & Perspectives|December 7, 2018
Risdiplam distributes and increases SMN protein in both the central nervous system and peripheral organsAgnès Poirier, Marla Weetall, Katja Heinig, et al.
Drug Metabolism and Disposition: the Biological Fate of Chemicals|October 8, 2021
Addressing Today's Absorption, Distribution, Metabolism, and Excretion (ADME) Challenges in the Translation of In Vitro ADME Characteristics to Humans: A Case Study of the <i>SMN2</i> mRNA Splicing Modifier RisdiplamStephen Fowler, Andreas Brink, Yumi Cleary, et al.
Medrxiv : the Preprint Server for Health Sciences|January 20, 2021
Enisamium is an inhibitor of the SARS-CoV-2 RNA polymerase and shows improvement of recovery in COVID-19 patients in an interim analysis of a clinical trialOlha Holubovska, Denisa Bojkova, Stefano Elli, et al.
Annals of Clinical and Translational Neurology|November 24, 2020
Risdiplam treatment has not led to retinal toxicity in patients with spinal muscular atrophyRobert C Sergott, Giulia M Amorelli, Giovanni Baranello, et al.
Nucleic Acid Therapeutics|May 30, 2025
Developmental and Reproductive Toxicity Testing Strategies for Oligonucleotides: A Workshop ProceedingsBethany R Hannas, Sara M Bender, Eileen Blasi, et al.
Journal of Medicinal Chemistry|June 15, 2016
Specific Correction of Alternative Survival Motor Neuron 2 Splicing by Small Molecules: Discovery of a Potential Novel Medicine To Treat Spinal Muscular AtrophyHasane Ratni, Gary M Karp, Marla Weetall, et al.
Journal of Medicinal Chemistry|July 26, 2018
Discovery of Risdiplam, a Selective Survival of Motor Neuron-2 ( SMN2) Gene Splicing Modifier for the Treatment of Spinal Muscular Atrophy (SMA)Hasane Ratni, Martin Ebeling, John Baird, et al.
Pageof 3