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Mégane Brusson

Showing results (1-10 of 12) with videos related to

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Progress in Molecular Biology and Translational Science|June 27, 2021
Genome editing approaches to β-hemoglobinopathiesMégane Brusson, Annarita Miccio
Frontiers in Genome Editing|October 29, 2021
Base and Prime Editing Technologies for Blood DisordersPanagiotis Antoniou, Annarita Miccio, Mégane Brusson
Stem Cells Translational Medicine|September 1, 2022
CRISPRthripsis: The Risk of CRISPR/Cas9-induced Chromothripsis in Gene TherapyMario Amendola, Mégane Brusson, Annarita Miccio
Thrombosis Research|May 28, 2014
Abnormal adhesion of red blood cells in polycythemia vera: a prothrombotic effect?Wassim El Nemer, Maria De Grandis, Mégane Brusson
Molecular Therapy : the Journal of the American Society of Gene Therapy|March 11, 2023
An optimized SpCas9 high-fidelity variant for direct protein deliveryEleonora Pedrazzoli, Andrea Bianchi, Alessandro Umbach, et al.
International Journal of Molecular Sciences|April 3, 2021
ABCG2 Is Overexpressed on Red Blood Cells in Ph-Negative Myeloproliferative Neoplasms and Potentiates Ruxolitinib-Induced ApoptosisRalfs Buks, Mégane Brusson, Sylvie Cochet, et al.
Molecular Therapy. Nucleic Acids|April 24, 2023
Novel lentiviral vectors for gene therapy of sickle cell disease combining gene addition and gene silencing strategiesMégane Brusson, Anne Chalumeau, Pierre Martinucci, et al.
Blood|August 26, 2025
A prime editing strategy to rewrite the γ-globin promoters and reactivate fetal hemoglobin for sickle cell diseaseAnne Chalumeau, Maria Bou Dames, Letizia Fontana, et al.
Molecular Therapy. Nucleic Acids|July 6, 2026
Enhanced γ-globin reactivation and sickle cell correction through a repressor-to-activator motif switch in the <i>HBG1/2</i> promotersAnne Chalumeau, Panagiotis Antoniou, Maria Bou Dames, et al.
Haematologica|March 31, 2018
Impact of hydroxycarbamide and interferon-α on red cell adhesion and membrane protein expression in polycythemia veraMégane Brusson, Maria De Grandis, Sylvie Cochet, et al.
Pageof 2

Showing results (1-10 of 12) with videos related to

Sort By:
Pageof 2
Progress in Molecular Biology and Translational Science|June 27, 2021
Genome editing approaches to β-hemoglobinopathiesMégane Brusson, Annarita Miccio
Frontiers in Genome Editing|October 29, 2021
Base and Prime Editing Technologies for Blood DisordersPanagiotis Antoniou, Annarita Miccio, Mégane Brusson
Stem Cells Translational Medicine|September 1, 2022
CRISPRthripsis: The Risk of CRISPR/Cas9-induced Chromothripsis in Gene TherapyMario Amendola, Mégane Brusson, Annarita Miccio
Thrombosis Research|May 28, 2014
Abnormal adhesion of red blood cells in polycythemia vera: a prothrombotic effect?Wassim El Nemer, Maria De Grandis, Mégane Brusson
Molecular Therapy : the Journal of the American Society of Gene Therapy|March 11, 2023
An optimized SpCas9 high-fidelity variant for direct protein deliveryEleonora Pedrazzoli, Andrea Bianchi, Alessandro Umbach, et al.
International Journal of Molecular Sciences|April 3, 2021
ABCG2 Is Overexpressed on Red Blood Cells in Ph-Negative Myeloproliferative Neoplasms and Potentiates Ruxolitinib-Induced ApoptosisRalfs Buks, Mégane Brusson, Sylvie Cochet, et al.
Molecular Therapy. Nucleic Acids|April 24, 2023
Novel lentiviral vectors for gene therapy of sickle cell disease combining gene addition and gene silencing strategiesMégane Brusson, Anne Chalumeau, Pierre Martinucci, et al.
Blood|August 26, 2025
A prime editing strategy to rewrite the γ-globin promoters and reactivate fetal hemoglobin for sickle cell diseaseAnne Chalumeau, Maria Bou Dames, Letizia Fontana, et al.
Molecular Therapy. Nucleic Acids|July 6, 2026
Enhanced γ-globin reactivation and sickle cell correction through a repressor-to-activator motif switch in the <i>HBG1/2</i> promotersAnne Chalumeau, Panagiotis Antoniou, Maria Bou Dames, et al.
Haematologica|March 31, 2018
Impact of hydroxycarbamide and interferon-α on red cell adhesion and membrane protein expression in polycythemia veraMégane Brusson, Maria De Grandis, Sylvie Cochet, et al.
Pageof 2