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Molecular Neurobiology|April 20, 2017
MicroRNA Metabolism and Dysregulation in Amyotrophic Lateral SclerosisPaola Rinchetti, Mafalda Rizzuti, Irene Faravelli, et al.Drug Discovery Today|October 4, 2014
Therapeutic applications of the cell-penetrating HIV-1 Tat peptideMafalda Rizzuti, Monica Nizzardo, Chiara Zanetta, et al.Journal of Cellular and Molecular Medicine|May 9, 2024
Charcot-Marie-Tooth type 2A in vivo models: Current updatesElena Abati, Mafalda Rizzuti, Alessia Anastasia, et al.International Journal of Molecular Sciences|January 11, 2018
Investigation of New Morpholino Oligomers to Increase Survival Motor Neuron Protein Levels in Spinal Muscular AtrophyAgnese Ramirez, Sebastiano G Crisafulli, Mafalda Rizzuti, et al.Stem Cell Reports|November 14, 2025
Advances and challenges in modeling Charcot-Marie-Tooth type 2A using iPSC-derived modelsMafalda Rizzuti, Elisa Pagliari, Martina D'Agostino, et al.Molecular Therapy : the Journal of the American Society of Gene Therapy|November 22, 2021
Cell-penetrating peptide-conjugated Morpholino rescues SMA in a symptomatic preclinical modelMargherita Bersani, Mafalda Rizzuti, Elisa Pagliari, et al.Scientific Reports|July 6, 2018
MicroRNA expression analysis identifies a subset of downregulated miRNAs in ALS motor neuron progenitorsMafalda Rizzuti, Giuseppe Filosa, Valentina Melzi, et al.Brain Communications|March 31, 2025
Unveiling amyotrophic lateral sclerosis complexity: insights from proteomics, metabolomics and microbiomicsSimone Scarcella, Lorenzo Brambilla, Lorenzo Quetti, et al.FASEB Journal : Official Publication of the Federation of American Societies for Experimental Biology|February 14, 2025
iPSC-derived human cortical organoids display profound alterations of cellular homeostasis following SARS-CoV-2 infection and Spike protein exposureGioia Cappelletti, Lorenzo Brambilla, Sergio Strizzi, et al.Molecular Neurobiology|February 9, 2024
Shaping the Neurovascular Unit Exploiting Human Brain OrganoidsMafalda Rizzuti, Valentina Melzi, Lorenzo Brambilla, et al.Pageof 3