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Neurology
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May 5, 2026
Age-Specific Parkinson Disease Risk in Gaucher Disease Type 1: Data From the ICGG Gaucher Registry
Roy N Alcalay, Pramod Mistry, Alessio Di Fonzo, et al.
Molecular Genetics and Metabolism
|
January 1, 2022
Screening, patient identification, evaluation, and treatment in patients with Gaucher disease: Results from a Delphi consensus
Priya S Kishnani, Walla Al-Hertani, Manisha Balwani, et al.
JIMD Reports
|
January 21, 2021
Pregnancy outcome in women with Gaucher disease type 1 who had unplanned pregnancies during eliglustat clinical trials
Elena Lukina, Manisha Balwani, Nadia Belmatoug, et al.
The New England Journal of Medicine
|
April 12, 2023
Dersimelagon in Erythropoietic Protoporphyrias
Manisha Balwani, Herbert L Bonkovsky, Cynthia Levy, et al.
Hepatology (Baltimore, Md.)
|
June 13, 2017
Acute hepatic porphyrias: Recommendations for evaluation and long-term management
Manisha Balwani, Bruce Wang, Karl E Anderson, et al.
Molecular Genetics and Metabolism Reports
|
November 21, 2022
A pilot study of oral iron therapy in erythropoietic protoporphyria and X-linked protoporphyria
Manisha Balwani, Hetanshi Naik, Jessica R Overbey, et al.
Journal of the American Academy of Dermatology
|
December 13, 2025
Bitopertin shows efficacy in patients with erythropoietic protoporphyria: Results from the randomized, double-blind, placebo-controlled AURORA trial
Amy K Yeung, Herbert L Bonkovsky, Manisha Balwani, et al.
Molecular Genetics and Metabolism
|
November 5, 2018
Strong correlation of ferrochelatase enzymatic activity with Mitoferrin-1 mRNA in lymphoblasts of patients with protoporphyria
John Phillips, Collin Farrell, Yongming Wang, et al.
Human Mutation
|
August 20, 2016
Acute Intermittent Porphyria: Predicted Pathogenicity of HMBS Variants Indicates Extremely Low Penetrance of the Autosomal Dominant Disease
Brenden Chen, Constanza Solis-Villa, Jörg Hakenberg, et al.
Blood Cells, Molecules & Diseases
|
November 12, 2010
The incidence of Parkinsonism in patients with type 1 Gaucher disease: data from the ICGG Gaucher Registry
Barry Rosenbloom, Manisha Balwani, Jeff M Bronstein, et al.
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Search research articles
Search
Showing results (51-60 of 94) with videos related to
Sort By:
Page
of 10
Neurology
|
May 5, 2026
Age-Specific Parkinson Disease Risk in Gaucher Disease Type 1: Data From the ICGG Gaucher Registry
Roy N Alcalay, Pramod Mistry, Alessio Di Fonzo, et al.
Molecular Genetics and Metabolism
|
January 1, 2022
Screening, patient identification, evaluation, and treatment in patients with Gaucher disease: Results from a Delphi consensus
Priya S Kishnani, Walla Al-Hertani, Manisha Balwani, et al.
JIMD Reports
|
January 21, 2021
Pregnancy outcome in women with Gaucher disease type 1 who had unplanned pregnancies during eliglustat clinical trials
Elena Lukina, Manisha Balwani, Nadia Belmatoug, et al.
The New England Journal of Medicine
|
April 12, 2023
Dersimelagon in Erythropoietic Protoporphyrias
Manisha Balwani, Herbert L Bonkovsky, Cynthia Levy, et al.
Hepatology (Baltimore, Md.)
|
June 13, 2017
Acute hepatic porphyrias: Recommendations for evaluation and long-term management
Manisha Balwani, Bruce Wang, Karl E Anderson, et al.
Molecular Genetics and Metabolism Reports
|
November 21, 2022
A pilot study of oral iron therapy in erythropoietic protoporphyria and X-linked protoporphyria
Manisha Balwani, Hetanshi Naik, Jessica R Overbey, et al.
Journal of the American Academy of Dermatology
|
December 13, 2025
Bitopertin shows efficacy in patients with erythropoietic protoporphyria: Results from the randomized, double-blind, placebo-controlled AURORA trial
Amy K Yeung, Herbert L Bonkovsky, Manisha Balwani, et al.
Molecular Genetics and Metabolism
|
November 5, 2018
Strong correlation of ferrochelatase enzymatic activity with Mitoferrin-1 mRNA in lymphoblasts of patients with protoporphyria
John Phillips, Collin Farrell, Yongming Wang, et al.
Human Mutation
|
August 20, 2016
Acute Intermittent Porphyria: Predicted Pathogenicity of HMBS Variants Indicates Extremely Low Penetrance of the Autosomal Dominant Disease
Brenden Chen, Constanza Solis-Villa, Jörg Hakenberg, et al.
Blood Cells, Molecules & Diseases
|
November 12, 2010
The incidence of Parkinsonism in patients with type 1 Gaucher disease: data from the ICGG Gaucher Registry
Barry Rosenbloom, Manisha Balwani, Jeff M Bronstein, et al.
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of 10