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Journal of Neurology|February 15, 2025
Patisiran in ATTRv amyloidosis with polyneuropathy: "PatisiranItaly" multicenter observational studyVincenzo Di Stefano, Pietro Guaraldi, Angela Romano, et al.European Journal of Neurology|June 2, 2026
Deep Phenotyping of F64L Mutation in a Multicentric Cohort of Patisiran-Treated Hereditary Transthyretin Amyloidosis Patients (Patisiranitaly)Marco Ceccanti, Pietro Guaraldi, Angela Romano, et al.Pageof 7