Showing results (21-30 of 68) with videos related to

Sort By:
Pageof 7
Orphanet Journal of Rare Diseases|February 15, 2017
Early disease progression of Hurler syndromeBridget T Kiely, Jennifer L Kohler, Hannah Y Coletti, et al.
JIMD Reports|January 24, 2015
Long-term functional outcomes of children with hurler syndrome treated with unrelated umbilical cord blood transplantationHannah Y Coletti, Mieke Aldenhoven, Karina Yelin, et al.
Biology of Blood and Marrow Transplantation : Journal of the American Society for Blood and Marrow Transplantation|January 26, 2013
Neurodevelopmental outcomes of umbilical cord blood transplantation in metachromatic leukodystrophyHolly R Martin, Michele D Poe, James M Provenzale, et al.
Clinical Trials (London, England)|May 7, 2019
The FOsmetpantotenate Replacement Therapy (FORT) randomized, double-blind, Placebo-controlled pivotal trial: Study design and development methodology of a novel primary efficacy outcome in patients with pantothenate kinase-associated neurodegenerationThomas Klopstock, Maria L Escolar, Randall D Marshall, et al.
Molecular Genetics and Metabolism|November 25, 2017
Practical management of behavioral problems in mucopolysaccharidoses disordersMaria L Escolar, Simon A Jones, Elsa G Shapiro, et al.
Proceedings. IEEE International Symposium on Biomedical Imaging|October 31, 2014
PARAMETRIC REGRESSION SCHEME FOR DISTRIBUTIONS: ANALYSIS OF DTI FIBER TRACT DIFFUSION CHANGES IN EARLY BRAIN DEVELOPMENTAnuja Sharma, P Thomas Fletcher, John H Gilmore, et al.
Proceedings. IEEE International Symposium on Biomedical Imaging|January 21, 2014
SPATIOTEMPORAL MODELING OF DISCRETE-TIME DISTRIBUTION-VALUED DATA APPLIED TO DTI TRACT EVOLUTION IN INFANT NEURODEVELOPMENTAnuja Sharma, P Thomas Fletcher, John H Gilmore, et al.
Molecular Genetics and Metabolism|November 21, 2017
Treatment of brain disease in the mucopolysaccharidosesMaurizio Scarpa, Paul J Orchard, Angela Schulz, et al.
Physical Therapy|June 8, 2007
Temporal and spatial gait characteristics of children with Hurler syndrome after umbilical cord blood transplantationStacey C Dusing, Deborah E Thorpe, Vicki S Mercer, et al.
Physical Therapy|September 6, 2007
Gross motor development of children with hurler syndrome after umbilical cord blood transplantationStacey C Dusing, Deborah E Thorpe, Michele D Poe, et al.
Pageof 7