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The Journal of Clinical Investigation|April 24, 2012
Lentiviral vector integration in the human genome induces alternative splicing and generates aberrant transcriptsArianna Moiani, Ylenia Paleari, Daniela Sartori, et al.
Blood|September 14, 2018
Transferrin receptor 2 is a potential novel therapeutic target for β-thalassemia: evidence from a murine modelIrene Artuso, Maria Rosa Lidonnici, Sandro Altamura, et al.
Haematologica|February 29, 2020
NCOA4-mediated ferritinophagy in macrophages is crucial to sustain erythropoiesis in miceAntonella Nai, Maria Rosa Lidonnici, Giorgia Federico, et al.
Blood|April 29, 2020
Hematopoietic stem cell function in β-thalassemia is impaired and is rescued by targeting the bone marrow nicheAnnamaria Aprile, Alessandro Gulino, Mariangela Storto, et al.
American Journal of Hematology|September 8, 2022
Transferrin receptor 2 (Tfr2) genetic deletion makes transfusion-independent a murine model of transfusion-dependent β-thalassemiaSimona Maria Di Modica, Emanuele Tanzi, Violante Olivari, et al.
Blood|March 25, 2026
Iron overload damages mitochondria and induces metabolic rewiring of hematopoietic stem cells towards glycolysisSilvia Sighinolfi, Laura Cassina, Maria Rosa Lidonnici, et al.
Molecular Therapy. Methods & Clinical Development|October 16, 2018
Multiple Integrated Non-clinical Studies Predict the Safety of Lentivirus-Mediated Gene Therapy for β-ThalassemiaMaria Rosa Lidonnici, Ylenia Paleari, Francesca Tiboni, et al.
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