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The Journal of Clinical Investigation|April 24, 2012
Lentiviral vector integration in the human genome induces alternative splicing and generates aberrant transcriptsArianna Moiani, Ylenia Paleari, Daniela Sartori, et al.Blood|September 14, 2018
Transferrin receptor 2 is a potential novel therapeutic target for β-thalassemia: evidence from a murine modelIrene Artuso, Maria Rosa Lidonnici, Sandro Altamura, et al.Stem Cell Reports|March 24, 2017
Efficient Ex Vivo Engineering and Expansion of Highly Purified Human Hematopoietic Stem and Progenitor Cell Populations for Gene TherapyErika Zonari, Giacomo Desantis, Carolina Petrillo, et al.Haematologica|February 29, 2020
NCOA4-mediated ferritinophagy in macrophages is crucial to sustain erythropoiesis in miceAntonella Nai, Maria Rosa Lidonnici, Giorgia Federico, et al.Blood|April 29, 2020
Hematopoietic stem cell function in β-thalassemia is impaired and is rescued by targeting the bone marrow nicheAnnamaria Aprile, Alessandro Gulino, Mariangela Storto, et al.American Journal of Hematology|September 8, 2022
Transferrin receptor 2 (Tfr2) genetic deletion makes transfusion-independent a murine model of transfusion-dependent β-thalassemiaSimona Maria Di Modica, Emanuele Tanzi, Violante Olivari, et al.Cancer Research|October 7, 2010
Expression of the transcriptional repressor Gfi-1 is regulated by C/EBP{alpha} and is involved in its proliferation and colony formation-inhibitory effects in p210BCR/ABL-expressing cellsMaria Rosa Lidonnici, Alessandra Audia, Angela Rachele Soliera, et al.Blood|March 25, 2026
Iron overload damages mitochondria and induces metabolic rewiring of hematopoietic stem cells towards glycolysisSilvia Sighinolfi, Laura Cassina, Maria Rosa Lidonnici, et al.Kidney International|March 29, 2023
A single approach to targeting transferrin receptor 2 corrects iron and erythropoietic defects in murine models of anemia of inflammation and chronic kidney diseaseViolante Olivari, Simona Maria Di Modica, Maria Rosa Lidonnici, et al.Molecular Therapy. Methods & Clinical Development|October 16, 2018
Multiple Integrated Non-clinical Studies Predict the Safety of Lentivirus-Mediated Gene Therapy for β-ThalassemiaMaria Rosa Lidonnici, Ylenia Paleari, Francesca Tiboni, et al.Pageof 3