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Molecular Genetics and Metabolism
|
July 9, 2026
Severe adenylosuccinate lyase deficiency with early autonomic dysfunction: functional characterization of a novel ADSL variant and exploratory treatment with disulfiram
Ružica Kravljanac, Marie Zikanova, Iva Milačić, et al.
Molecular Genetics and Metabolism
|
February 12, 2013
Genetic and metabolomic analysis of AdeD and AdeI mutants of de novo purine biosynthesis: cellular models of de novo purine biosynthesis deficiency disorders
Nathan Duval, Kyleen Luhrs, Terry G Wilkinson, et al.
Journal of Inherited Metabolic Disease
|
May 27, 2025
Phosphoribosylformylglycinamidine Synthase (PFAS) Deficiency: Clinical, Genetic and Metabolic Characterisation of a Novel Defect in Purine de Novo Synthesis
Marie Zikanova, Vaclava Skopova, Kyra E Stuurman, et al.
Molecular Genetics and Metabolism
|
June 6, 2008
Clinical, biochemical and molecular findings in seven Polish patients with adenylosuccinate lyase deficiency
Agnieszka Jurecka, Marie Zikanova, Anna Tylki-Szymanska, et al.
European Journal of Human Genetics : EJHG
|
November 28, 2024
Expanding clinical spectrum of PAICS deficiency: Comprehensive analysis of two sibling cases
Wen-Chin Weng, Vaclava Skopova, Veronika Baresova, et al.
Human Molecular Genetics
|
October 11, 2019
PAICS deficiency, a new defect of de novo purine synthesis resulting in multiple congenital anomalies and fatal outcome
Anna Pelet, Vaclava Skopova, Ulrike Steuerwald, et al.
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Search research articles
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Showing results (11-20 of 16) with videos related to
Sort By:
Page
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You have reached the last page of results.
This site can display upto 16 results.
Molecular Genetics and Metabolism
|
July 9, 2026
Severe adenylosuccinate lyase deficiency with early autonomic dysfunction: functional characterization of a novel ADSL variant and exploratory treatment with disulfiram
Ružica Kravljanac, Marie Zikanova, Iva Milačić, et al.
Molecular Genetics and Metabolism
|
February 12, 2013
Genetic and metabolomic analysis of AdeD and AdeI mutants of de novo purine biosynthesis: cellular models of de novo purine biosynthesis deficiency disorders
Nathan Duval, Kyleen Luhrs, Terry G Wilkinson, et al.
Journal of Inherited Metabolic Disease
|
May 27, 2025
Phosphoribosylformylglycinamidine Synthase (PFAS) Deficiency: Clinical, Genetic and Metabolic Characterisation of a Novel Defect in Purine de Novo Synthesis
Marie Zikanova, Vaclava Skopova, Kyra E Stuurman, et al.
Molecular Genetics and Metabolism
|
June 6, 2008
Clinical, biochemical and molecular findings in seven Polish patients with adenylosuccinate lyase deficiency
Agnieszka Jurecka, Marie Zikanova, Anna Tylki-Szymanska, et al.
European Journal of Human Genetics : EJHG
|
November 28, 2024
Expanding clinical spectrum of PAICS deficiency: Comprehensive analysis of two sibling cases
Wen-Chin Weng, Vaclava Skopova, Veronika Baresova, et al.
Human Molecular Genetics
|
October 11, 2019
PAICS deficiency, a new defect of de novo purine synthesis resulting in multiple congenital anomalies and fatal outcome
Anna Pelet, Vaclava Skopova, Ulrike Steuerwald, et al.
Page
of 2