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Elife
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September 20, 2021
SMA-miRs (miR-181a-5p, -324-5p, and -451a) are overexpressed in spinal muscular atrophy skeletal muscle and serum samples
Emanuela Abiusi, Paola Infante, Cinzia Cagnoli, et al.
Journal of Clinical Lipidology
|
February 13, 2026
Heterogeneous nature of severe hypertriglyceridemia in childhood
María José Ariza, José Rioja, Verónica Adriana Seidel, et al.
Genes
|
October 31, 2018
Copy Number Variants Account for a Tiny Fraction of Undiagnosed Myopathic Patients
Teresa Giugliano, Marco Savarese, Arcomaria Garofalo, et al.
Neurobiology of Aging
|
September 6, 2016
Rare variants in SQSTM1 and VCP genes and risk of sporadic inclusion body myositis
Qiang Gang, Conceição Bettencourt, Pedro M Machado, et al.
Muscle & Nerve
|
May 18, 2016
The italian limb girdle muscular dystrophy registry: Relative frequency, clinical features, and differential diagnosis
Francesca Magri, Vincenzo Nigro, Corrado Angelini, et al.
Orphanet Journal of Rare Diseases
|
September 28, 2018
Broad phenotypic spectrum and genotype-phenotype correlations in GMPPB-related dystroglycanopathies: an Italian cross-sectional study
Guja Astrea, Alessandro Romano, Corrado Angelini, et al.
European Journal of Human Genetics : EJHG
|
December 25, 2014
The EuroBioBank Network: 10 years of hands-on experience of collaborative, transnational biobanking for rare diseases
Marina Mora, Corrado Angelini, Fabrizia Bignami, et al.
Journal of Neurology
|
May 11, 2015
Centronuclear myopathies: genotype-phenotype correlation and frequency of defined genetic forms in an Italian cohort
Fabiana Fattori, Lorenzo Maggi, Claudio Bruno, et al.
JAMA Neurology
|
February 14, 2018
Interpreting Genetic Variants in Titin in Patients With Muscle Disorders
Marco Savarese, Lorenzo Maggi, Anna Vihola, et al.
Frontiers in Genetics
|
March 21, 2020
The Genetic Landscape of Dystrophin Mutations in Italy: A Nationwide Study
Marcella Neri, Rachele Rossi, Cecilia Trabanelli, et al.
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of 13
Search research articles
Search
Showing results (111-120 of 122) with videos related to
Sort By:
Page
of 13
Elife
|
September 20, 2021
SMA-miRs (miR-181a-5p, -324-5p, and -451a) are overexpressed in spinal muscular atrophy skeletal muscle and serum samples
Emanuela Abiusi, Paola Infante, Cinzia Cagnoli, et al.
Journal of Clinical Lipidology
|
February 13, 2026
Heterogeneous nature of severe hypertriglyceridemia in childhood
María José Ariza, José Rioja, Verónica Adriana Seidel, et al.
Genes
|
October 31, 2018
Copy Number Variants Account for a Tiny Fraction of Undiagnosed Myopathic Patients
Teresa Giugliano, Marco Savarese, Arcomaria Garofalo, et al.
Neurobiology of Aging
|
September 6, 2016
Rare variants in SQSTM1 and VCP genes and risk of sporadic inclusion body myositis
Qiang Gang, Conceição Bettencourt, Pedro M Machado, et al.
Muscle & Nerve
|
May 18, 2016
The italian limb girdle muscular dystrophy registry: Relative frequency, clinical features, and differential diagnosis
Francesca Magri, Vincenzo Nigro, Corrado Angelini, et al.
Orphanet Journal of Rare Diseases
|
September 28, 2018
Broad phenotypic spectrum and genotype-phenotype correlations in GMPPB-related dystroglycanopathies: an Italian cross-sectional study
Guja Astrea, Alessandro Romano, Corrado Angelini, et al.
European Journal of Human Genetics : EJHG
|
December 25, 2014
The EuroBioBank Network: 10 years of hands-on experience of collaborative, transnational biobanking for rare diseases
Marina Mora, Corrado Angelini, Fabrizia Bignami, et al.
Journal of Neurology
|
May 11, 2015
Centronuclear myopathies: genotype-phenotype correlation and frequency of defined genetic forms in an Italian cohort
Fabiana Fattori, Lorenzo Maggi, Claudio Bruno, et al.
JAMA Neurology
|
February 14, 2018
Interpreting Genetic Variants in Titin in Patients With Muscle Disorders
Marco Savarese, Lorenzo Maggi, Anna Vihola, et al.
Frontiers in Genetics
|
March 21, 2020
The Genetic Landscape of Dystrophin Mutations in Italy: A Nationwide Study
Marcella Neri, Rachele Rossi, Cecilia Trabanelli, et al.
Page
of 13