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Journal of Medical Genetics
|
October 3, 2023
Spectrum of <i>LYST</i> mutations in Chediak-Higashi syndrome: a report of novel variants and a comprehensive review of the literature
Marie Morimoto, Elena-Raluca Nicoli, Chulaluck Kuptanon, et al.
Gastroenterology
|
October 9, 2012
Characteristics of congenital hepatic fibrosis in a large cohort of patients with autosomal recessive polycystic kidney disease
Meral Gunay-Aygun, Esperanza Font-Montgomery, Linda Lukose, et al.
Genetics in Medicine : Official Journal of the American College of Medical Genetics
|
July 14, 2021
Safety and efficacy of N-acetylmannosamine (ManNAc) in patients with GNE myopathy: an open-label phase 2 study
Nuria Carrillo, May C Malicdan, Petcharat Leoyklang, et al.
Nature Genetics
|
July 19, 2011
NBEAL2 is mutated in gray platelet syndrome and is required for biogenesis of platelet α-granules
Meral Gunay-Aygun, Tzipora C Falik-Zaccai, Thierry Vilboux, et al.
Journal of Medical Genetics
|
April 21, 2016
Cystic cerebellar dysplasia and biallelic LAMA1 mutations: a lamininopathy associated with tics, obsessive compulsive traits and myopia due to cell adhesion and migration defects
Thierry Vilboux, May Christine V Malicdan, Yun Min Chang, et al.
Nature Genetics
|
August 16, 2011
Exome sequencing identifies ACSF3 as a cause of combined malonic and methylmalonic aciduria
Jennifer L Sloan, Jennifer J Johnston, Irini Manoli, et al.
Molecular Genetics and Metabolism
|
May 7, 2015
Expanding the clinical and molecular characteristics of PIGT-CDG, a disorder of glycosylphosphatidylinositol anchors
Christina Lam, Gretchen A Golas, Mariska Davids, et al.
The New England Journal of Medicine
|
June 7, 2013
A congenital neutrophil defect syndrome associated with mutations in VPS45
Thierry Vilboux, Atar Lev, May Christine V Malicdan, et al.
Blood
|
August 17, 2010
Gray platelet syndrome: natural history of a large patient cohort and locus assignment to chromosome 3p
Meral Gunay-Aygun, Yifat Zivony-Elboum, Fatma Gumruk, et al.
The New England Journal of Medicine
|
June 5, 2009
An autoinflammatory disease with deficiency of the interleukin-1-receptor antagonist
Ivona Aksentijevich, Seth L Masters, Polly J Ferguson, et al.
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Search research articles
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Showing results (121-130 of 130) with videos related to
Sort By:
Page
of 13
You have reached the last page of results.
This site can display upto 130 results.
Journal of Medical Genetics
|
October 3, 2023
Spectrum of <i>LYST</i> mutations in Chediak-Higashi syndrome: a report of novel variants and a comprehensive review of the literature
Marie Morimoto, Elena-Raluca Nicoli, Chulaluck Kuptanon, et al.
Gastroenterology
|
October 9, 2012
Characteristics of congenital hepatic fibrosis in a large cohort of patients with autosomal recessive polycystic kidney disease
Meral Gunay-Aygun, Esperanza Font-Montgomery, Linda Lukose, et al.
Genetics in Medicine : Official Journal of the American College of Medical Genetics
|
July 14, 2021
Safety and efficacy of N-acetylmannosamine (ManNAc) in patients with GNE myopathy: an open-label phase 2 study
Nuria Carrillo, May C Malicdan, Petcharat Leoyklang, et al.
Nature Genetics
|
July 19, 2011
NBEAL2 is mutated in gray platelet syndrome and is required for biogenesis of platelet α-granules
Meral Gunay-Aygun, Tzipora C Falik-Zaccai, Thierry Vilboux, et al.
Journal of Medical Genetics
|
April 21, 2016
Cystic cerebellar dysplasia and biallelic LAMA1 mutations: a lamininopathy associated with tics, obsessive compulsive traits and myopia due to cell adhesion and migration defects
Thierry Vilboux, May Christine V Malicdan, Yun Min Chang, et al.
Nature Genetics
|
August 16, 2011
Exome sequencing identifies ACSF3 as a cause of combined malonic and methylmalonic aciduria
Jennifer L Sloan, Jennifer J Johnston, Irini Manoli, et al.
Molecular Genetics and Metabolism
|
May 7, 2015
Expanding the clinical and molecular characteristics of PIGT-CDG, a disorder of glycosylphosphatidylinositol anchors
Christina Lam, Gretchen A Golas, Mariska Davids, et al.
The New England Journal of Medicine
|
June 7, 2013
A congenital neutrophil defect syndrome associated with mutations in VPS45
Thierry Vilboux, Atar Lev, May Christine V Malicdan, et al.
Blood
|
August 17, 2010
Gray platelet syndrome: natural history of a large patient cohort and locus assignment to chromosome 3p
Meral Gunay-Aygun, Yifat Zivony-Elboum, Fatma Gumruk, et al.
The New England Journal of Medicine
|
June 5, 2009
An autoinflammatory disease with deficiency of the interleukin-1-receptor antagonist
Ivona Aksentijevich, Seth L Masters, Polly J Ferguson, et al.
Page
of 13