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Massimo Pifferi

Showing results (41-50 of 48) with videos related to

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Journal of Medical Genetics|January 6, 2016
Gene editing of DNAH11 restores normal cilia motility in primary ciliary dyskinesiaMichele Lai, Massimo Pifferi, Andrew Bush, et al.
Human Gene Therapy|April 29, 2026
AAV-Mediated Base Editing for Correction of <i>RSPH4A</i> Mutations in Primary Ciliary Dyskinesia: A Proof-of-Concept StudyAlessandro De Carli, Sara Pastore, Debora Maj, et al.
The Lancet. Respiratory Medicine|September 3, 2023
Safety and efficacy of the epithelial sodium channel blocker idrevloride in people with primary ciliary dyskinesia (CLEAN-PCD): a multinational, phase 2, randomised, double-blind, placebo-controlled crossover trialFelix C Ringshausen, Adam J Shapiro, Kim G Nielsen, et al.
Frontiers in Molecular Biosciences|July 10, 2026
Pulmonary exacerbations in patients with genetically confirmed PCD: a prospective observational multicentre studyPinelopi Anagnostopoulou, Panayiotis Kouis, Dilber Ademhan Tural, et al.
ERJ Open Research|June 24, 2025
International consensus statement on routine blood testing in primary ciliary dyskinesiaSarah Altaraihi, June K Marthin, Pinelopi Anagnostopoulou, et al.
Italian Journal of Pediatrics|October 26, 2021
Prevention of recurrent respiratory infections : Inter-society ConsensusElena Chiappini, Francesca Santamaria, Gian Luigi Marseglia, et al.
ERJ Open Research|August 19, 2022
The disease-specific clinical trial network for primary ciliary dyskinesia: PCD-CTNJohanna Raidt, Bernard Maitre, Petra Pennekamp, et al.
The European Respiratory Journal|June 13, 2024
Analyses of 1236 genotyped primary ciliary dyskinesia individuals identify regional clusters of distinct DNA variants and significant genotype-phenotype correlationsJohanna Raidt, Sarah Riepenhausen, Petra Pennekamp, et al.
Pageof 5

Showing results (41-50 of 48) with videos related to

Sort By:
Pageof 5
You have reached the last page of results.This site can display upto 48 results.
Journal of Medical Genetics|January 6, 2016
Gene editing of DNAH11 restores normal cilia motility in primary ciliary dyskinesiaMichele Lai, Massimo Pifferi, Andrew Bush, et al.
Human Gene Therapy|April 29, 2026
AAV-Mediated Base Editing for Correction of <i>RSPH4A</i> Mutations in Primary Ciliary Dyskinesia: A Proof-of-Concept StudyAlessandro De Carli, Sara Pastore, Debora Maj, et al.
The Lancet. Respiratory Medicine|September 3, 2023
Safety and efficacy of the epithelial sodium channel blocker idrevloride in people with primary ciliary dyskinesia (CLEAN-PCD): a multinational, phase 2, randomised, double-blind, placebo-controlled crossover trialFelix C Ringshausen, Adam J Shapiro, Kim G Nielsen, et al.
Frontiers in Molecular Biosciences|July 10, 2026
Pulmonary exacerbations in patients with genetically confirmed PCD: a prospective observational multicentre studyPinelopi Anagnostopoulou, Panayiotis Kouis, Dilber Ademhan Tural, et al.
ERJ Open Research|June 24, 2025
International consensus statement on routine blood testing in primary ciliary dyskinesiaSarah Altaraihi, June K Marthin, Pinelopi Anagnostopoulou, et al.
Italian Journal of Pediatrics|October 26, 2021
Prevention of recurrent respiratory infections : Inter-society ConsensusElena Chiappini, Francesca Santamaria, Gian Luigi Marseglia, et al.
ERJ Open Research|August 19, 2022
The disease-specific clinical trial network for primary ciliary dyskinesia: PCD-CTNJohanna Raidt, Bernard Maitre, Petra Pennekamp, et al.
The European Respiratory Journal|June 13, 2024
Analyses of 1236 genotyped primary ciliary dyskinesia individuals identify regional clusters of distinct DNA variants and significant genotype-phenotype correlationsJohanna Raidt, Sarah Riepenhausen, Petra Pennekamp, et al.
Pageof 5