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Brain : a Journal of Neurology
|
January 17, 2021
Defective phosphatidylethanolamine biosynthesis leads to a broad ataxia-spasticity spectrum
Rauan Kaiyrzhanov, Saskia Wortmann, Taryn Reid, et al.
Brain : a Journal of Neurology
|
December 22, 2020
Early-onset phenotype of bi-allelic GRN mutations
Caroline Neuray, Tipu Sultan, Javeira Raza Alvi, et al.
American Journal of Human Genetics
|
December 30, 2019
Bi-Allelic UQCRFS1 Variants Are Associated with Mitochondrial Complex III Deficiency, Cardiomyopathy, and Alopecia Totalis
Mirjana Gusic, Gudrun Schottmann, René G Feichtinger, et al.
Parkinsonism & Related Disorders
|
July 7, 2020
Recessive null-allele variants in MAG associated with spastic ataxia, nystagmus, neuropathy, and dystonia
Michael Zech, Theresa Brunet, Matej Škorvánek, et al.
Pediatric Pulmonology
|
August 25, 2020
Rescue of respiratory failure in pulmonary alveolar proteinosis due to pathogenic MARS1 variants
Dominic Lenz, Mirjam Stahl, Elias Seidl, et al.
Journal of Inherited Metabolic Disease
|
May 20, 2025
Hepatic Form of Dihydrolipoamide Dehydrogenase Deficiency (DLDD): Phenotypic Spectrum, Laboratory Findings, and Therapeutic Approaches in 52 Patients
Nicole Hammann, Christian Staufner, Lea Dewi Schlieben, et al.
American Journal of Kidney Diseases : the Official Journal of the National Kidney Foundation
|
May 4, 2020
Exome Sequencing and Identification of Phenocopies in Patients With Clinically Presumed Hereditary Nephropathies
Korbinian M Riedhammer, Matthias C Braunisch, Roman Günthner, et al.
Human Genetics
|
December 15, 2021
Variant-specific effects define the phenotypic spectrum of HNRNPH2-associated neurodevelopmental disorders in males
Hans-Jürgen Kreienkamp, Matias Wagner, Heike Weigand, et al.
Nature Medicine
|
April 22, 2025
Antisense oligonucleotide treatment in a preterm infant with early-onset SCN2A developmental and epileptic encephalopathy
Matias Wagner, Géza Berecki, Walid Fazeli, et al.
Journal of Neurology
|
December 21, 2023
Next-generation sequencing and comprehensive data reassessment in 263 adult patients with neuromuscular disorders: insights into the gray zone of molecular diagnoses
Martin Krenn, Matias Wagner, Gudrun Zulehner, et al.
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of 19
Search research articles
Search
Showing results (81-90 of 188) with videos related to
Sort By:
Page
of 19
Brain : a Journal of Neurology
|
January 17, 2021
Defective phosphatidylethanolamine biosynthesis leads to a broad ataxia-spasticity spectrum
Rauan Kaiyrzhanov, Saskia Wortmann, Taryn Reid, et al.
Brain : a Journal of Neurology
|
December 22, 2020
Early-onset phenotype of bi-allelic GRN mutations
Caroline Neuray, Tipu Sultan, Javeira Raza Alvi, et al.
American Journal of Human Genetics
|
December 30, 2019
Bi-Allelic UQCRFS1 Variants Are Associated with Mitochondrial Complex III Deficiency, Cardiomyopathy, and Alopecia Totalis
Mirjana Gusic, Gudrun Schottmann, René G Feichtinger, et al.
Parkinsonism & Related Disorders
|
July 7, 2020
Recessive null-allele variants in MAG associated with spastic ataxia, nystagmus, neuropathy, and dystonia
Michael Zech, Theresa Brunet, Matej Škorvánek, et al.
Pediatric Pulmonology
|
August 25, 2020
Rescue of respiratory failure in pulmonary alveolar proteinosis due to pathogenic MARS1 variants
Dominic Lenz, Mirjam Stahl, Elias Seidl, et al.
Journal of Inherited Metabolic Disease
|
May 20, 2025
Hepatic Form of Dihydrolipoamide Dehydrogenase Deficiency (DLDD): Phenotypic Spectrum, Laboratory Findings, and Therapeutic Approaches in 52 Patients
Nicole Hammann, Christian Staufner, Lea Dewi Schlieben, et al.
American Journal of Kidney Diseases : the Official Journal of the National Kidney Foundation
|
May 4, 2020
Exome Sequencing and Identification of Phenocopies in Patients With Clinically Presumed Hereditary Nephropathies
Korbinian M Riedhammer, Matthias C Braunisch, Roman Günthner, et al.
Human Genetics
|
December 15, 2021
Variant-specific effects define the phenotypic spectrum of HNRNPH2-associated neurodevelopmental disorders in males
Hans-Jürgen Kreienkamp, Matias Wagner, Heike Weigand, et al.
Nature Medicine
|
April 22, 2025
Antisense oligonucleotide treatment in a preterm infant with early-onset SCN2A developmental and epileptic encephalopathy
Matias Wagner, Géza Berecki, Walid Fazeli, et al.
Journal of Neurology
|
December 21, 2023
Next-generation sequencing and comprehensive data reassessment in 263 adult patients with neuromuscular disorders: insights into the gray zone of molecular diagnoses
Martin Krenn, Matias Wagner, Gudrun Zulehner, et al.
Page
of 19