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Human Mutation|January 7, 2012
Rapid, comprehensive analysis of the dystrophin transcript by a custom micro-fluidic exome arrayMatteo Bovolenta, Chiara Scotton, Maria Sofia Falzarano, et al.Journal of Cellular Biochemistry|January 13, 2006
PLC-beta2 monitors the drug-induced release of differentiation blockade in tumoral myeloid precursorsFederica Brugnoli, Matteo Bovolenta, Mascia Benedusi, et al.Scientific Reports|June 25, 2016
An engineered tale-transcription factor rescues transcription of factor VII impaired by promoter mutations and enhances its endogenous expression in hepatocytesElena Barbon, Silvia Pignani, Alessio Branchini, et al.Molecular Therapy. Nucleic Acids|September 10, 2018
Ex Vivo COL7A1 Correction for Recessive Dystrophic Epidermolysis Bullosa Using CRISPR/Cas9 and Homology-Directed RepairAraksya Izmiryan, Clarisse Ganier, Matteo Bovolenta, et al.International Journal of Molecular Sciences|April 23, 2022
Antisense Oligonucleotides Conjugated with Lipophilic Compounds: Synthesis and In Vitro Evaluation of Exon Skipping in Duchenne Muscular DystrophyElena Marchesi, Rita Cortesi, Lorenzo Preti, et al.Molecules (Basel, Switzerland)|December 24, 2021
Synthesis and Exon-Skipping Properties of a 3'-Ursodeoxycholic Acid-Conjugated Oligonucleotide Targeting DMD Pre-mRNA: Pre-Synthetic versus Post-Synthetic ApproachElena Marchesi, Matteo Bovolenta, Lorenzo Preti, et al.Biochimica Et Biophysica Acta. Gene Regulatory Mechanisms|April 22, 2019
Tailoring the CRISPR system to transactivate coagulation gene promoters in normal and mutated contextsSilvia Pignani, Federico Zappaterra, Elena Barbon, et al.Biochimica Et Biophysica Acta. Molecular Basis of Disease|September 19, 2016
Exploring Splicing-Switching Molecules For Seckel Syndrome TherapyDaniela Scalet, Dario Balestra, Sara Rohban, et al.Pharmaceutics|August 29, 2024
In Vitro Studies to Evaluate the Intestinal Permeation of an Ursodeoxycholic Acid-Conjugated Oligonucleotide for Duchenne Muscular Dystrophy TreatmentMarika Faiella, Giada Botti, Alessandro Dalpiaz, et al.Muscle & Nerve|April 14, 2011
Macrophages: a minimally invasive tool for monitoring collagen VI myopathiesFrancesca Gualandi, Rosa Curci, Patrizia Sabatelli, et al.Pageof 4