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Human Mutation|January 7, 2012
Rapid, comprehensive analysis of the dystrophin transcript by a custom micro-fluidic exome arrayMatteo Bovolenta, Chiara Scotton, Maria Sofia Falzarano, et al.
Journal of Cellular Biochemistry|January 13, 2006
PLC-beta2 monitors the drug-induced release of differentiation blockade in tumoral myeloid precursorsFederica Brugnoli, Matteo Bovolenta, Mascia Benedusi, et al.
Scientific Reports|June 25, 2016
An engineered tale-transcription factor rescues transcription of factor VII impaired by promoter mutations and enhances its endogenous expression in hepatocytesElena Barbon, Silvia Pignani, Alessio Branchini, et al.
Molecular Therapy. Nucleic Acids|September 10, 2018
Ex Vivo COL7A1 Correction for Recessive Dystrophic Epidermolysis Bullosa Using CRISPR/Cas9 and Homology-Directed RepairAraksya Izmiryan, Clarisse Ganier, Matteo Bovolenta, et al.
International Journal of Molecular Sciences|April 23, 2022
Antisense Oligonucleotides Conjugated with Lipophilic Compounds: Synthesis and In Vitro Evaluation of Exon Skipping in Duchenne Muscular DystrophyElena Marchesi, Rita Cortesi, Lorenzo Preti, et al.
Molecules (Basel, Switzerland)|December 24, 2021
Synthesis and Exon-Skipping Properties of a 3'-Ursodeoxycholic Acid-Conjugated Oligonucleotide Targeting DMD Pre-mRNA: Pre-Synthetic versus Post-Synthetic ApproachElena Marchesi, Matteo Bovolenta, Lorenzo Preti, et al.
Biochimica Et Biophysica Acta. Molecular Basis of Disease|September 19, 2016
Exploring Splicing-Switching Molecules For Seckel Syndrome TherapyDaniela Scalet, Dario Balestra, Sara Rohban, et al.
Biochimica Et Biophysica Acta. Gene Regulatory Mechanisms|April 22, 2019
Tailoring the CRISPR system to transactivate coagulation gene promoters in normal and mutated contextsSilvia Pignani, Federico Zappaterra, Elena Barbon, et al.
Muscle & Nerve|April 14, 2011
Macrophages: a minimally invasive tool for monitoring collagen VI myopathiesFrancesca Gualandi, Rosa Curci, Patrizia Sabatelli, et al.
Pharmaceutics|August 29, 2024
In Vitro Studies to Evaluate the Intestinal Permeation of an Ursodeoxycholic Acid-Conjugated Oligonucleotide for Duchenne Muscular Dystrophy TreatmentMarika Faiella, Giada Botti, Alessandro Dalpiaz, et al.
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