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Matthew H Porteus

Showing results (91-100 of 141) with videos related to

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Neuron|October 17, 2024
Human assembloids reveal the consequences of CACNA1G gene variants in the thalamocortical pathwayJi-Il Kim, Yuki Miura, Min-Yin Li, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy|March 8, 2021
Improved Genome Editing through Inhibition of FANCM and Members of the BTR Dissolvase ComplexGustavo de Alencastro, Francesco Puzzo, Mara Pavel-Dinu, et al.
Nature Communications|December 15, 2019
Functional significance of U2AF1 S34F mutations in lung adenocarcinomasMohammad S Esfahani, Luke J Lee, Young-Jun Jeon, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy|July 15, 2018
Global Transcriptional Response to CRISPR/Cas9-AAV6-Based Genome Editing in CD34<sup>+</sup> Hematopoietic Stem and Progenitor CellsM Kyle Cromer, Sriram Vaidyanathan, Daniel E Ryan, et al.
Nature Biotechnology|June 30, 2015
Chemically modified guide RNAs enhance CRISPR-Cas genome editing in human primary cellsAyal Hendel, Rasmus O Bak, Joseph T Clark, et al.
Nature|November 8, 2016
CRISPR/Cas9 β-globin gene targeting in human haematopoietic stem cellsDaniel P Dever, Rasmus O Bak, Andreas Reinisch, et al.
Nature Communications|March 31, 2025
Multilayered HIV-1 resistance in HSPCs through CCR5 Knockout and B cell secretion of HIV-inhibiting antibodiesWilliam N Feist, Sofia E Luna, Kaya Ben-Efraim, et al.
Nature Communications|January 29, 2025
Engineering synthetic signaling receptors to enable erythropoietin-free erythropoiesisAadit P Shah, Kiran R Majeti, Freja K Ekman, et al.
Gene Therapy|March 13, 2021
Correction of X-CGD patient HSPCs by targeted CYBB cDNA insertion using CRISPR/Cas9 with 53BP1 inhibition for enhanced homology-directed repairColin L Sweeney, Mara Pavel-Dinu, Uimook Choi, et al.
Nature Communications|September 8, 2019
Human genome-edited hematopoietic stem cells phenotypically correct Mucopolysaccharidosis type INatalia Gomez-Ospina, Samantha G Scharenberg, Nathalie Mostrel, et al.
Pageof 15

Showing results (91-100 of 141) with videos related to

Sort By:
Pageof 15
Neuron|October 17, 2024
Human assembloids reveal the consequences of CACNA1G gene variants in the thalamocortical pathwayJi-Il Kim, Yuki Miura, Min-Yin Li, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy|March 8, 2021
Improved Genome Editing through Inhibition of FANCM and Members of the BTR Dissolvase ComplexGustavo de Alencastro, Francesco Puzzo, Mara Pavel-Dinu, et al.
Nature Communications|December 15, 2019
Functional significance of U2AF1 S34F mutations in lung adenocarcinomasMohammad S Esfahani, Luke J Lee, Young-Jun Jeon, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy|July 15, 2018
Global Transcriptional Response to CRISPR/Cas9-AAV6-Based Genome Editing in CD34<sup>+</sup> Hematopoietic Stem and Progenitor CellsM Kyle Cromer, Sriram Vaidyanathan, Daniel E Ryan, et al.
Nature Biotechnology|June 30, 2015
Chemically modified guide RNAs enhance CRISPR-Cas genome editing in human primary cellsAyal Hendel, Rasmus O Bak, Joseph T Clark, et al.
Nature|November 8, 2016
CRISPR/Cas9 β-globin gene targeting in human haematopoietic stem cellsDaniel P Dever, Rasmus O Bak, Andreas Reinisch, et al.
Nature Communications|March 31, 2025
Multilayered HIV-1 resistance in HSPCs through CCR5 Knockout and B cell secretion of HIV-inhibiting antibodiesWilliam N Feist, Sofia E Luna, Kaya Ben-Efraim, et al.
Nature Communications|January 29, 2025
Engineering synthetic signaling receptors to enable erythropoietin-free erythropoiesisAadit P Shah, Kiran R Majeti, Freja K Ekman, et al.
Gene Therapy|March 13, 2021
Correction of X-CGD patient HSPCs by targeted CYBB cDNA insertion using CRISPR/Cas9 with 53BP1 inhibition for enhanced homology-directed repairColin L Sweeney, Mara Pavel-Dinu, Uimook Choi, et al.
Nature Communications|September 8, 2019
Human genome-edited hematopoietic stem cells phenotypically correct Mucopolysaccharidosis type INatalia Gomez-Ospina, Samantha G Scharenberg, Nathalie Mostrel, et al.
Pageof 15