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Matthew H Porteus

Showing results (81-90 of 141) with videos related to

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Elife|June 7, 2023
Combined lineage tracing and scRNA-seq reveals unexpected first heart field predominance of human iPSC differentiationFrancisco X Galdos, Carissa Lee, Soah Lee, et al.
Nucleic Acids Research|June 1, 2019
Highly efficient editing of the β-globin gene in patient-derived hematopoietic stem and progenitor cells to treat sickle cell diseaseSo Hyun Park, Ciaran M Lee, Daniel P Dever, et al.
Blood Advances|November 7, 2025
Novel humanized loss-of-function NF1 mouse model of juvenile myelomonocytic leukemiaRoshani Sinha, Rachana V Patil, Rosa Romano, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy|February 20, 2021
Correction of recessive dystrophic epidermolysis bullosa by homology-directed repair-mediated genome editingJose Bonafont, Angeles Mencía, Esteban Chacón-Solano, et al.
Nature Communications|January 3, 2024
Transient inhibition of 53BP1 increases the frequency of targeted integration in human hematopoietic stem and progenitor cellsRon Baik, M Kyle Cromer, Steve E Glenn, et al.
Nature Communications|May 15, 2015
Editing the genome to introduce a beneficial naturally occurring mutation associated with increased fetal globinBeeke Wienert, Alister P W Funnell, Laura J Norton, et al.
Molecular Therapy. Nucleic Acids|September 10, 2018
Uridine Depletion and Chemical Modification Increase Cas9 mRNA Activity and Reduce Immunogenicity without HPLC PurificationSriram Vaidyanathan, Krist T Azizian, A K M Ashiqul Haque, et al.
Biorxiv : the Preprint Server for Biology|May 20, 2024
Dual α-globin and truncated EPO receptor knockin restores hemoglobin production in α-thalassemia-derived red blood cellsSimon N Chu, Eric Soupene, Beeke Wienert, et al.
Biorxiv : the Preprint Server for Biology|March 18, 2024
Combining Cell-Intrinsic and -Extrinsic Resistance to HIV-1 By Engineering Hematopoietic Stem Cells for CCR5 Knockout and B Cell Secretion of Therapeutic AntibodiesWilliam N Feist, Sofia E Luna, Kaya Ben-Efraim, et al.
Cell Stem Cell|June 23, 2009
Gene targeting of a disease-related gene in human induced pluripotent stem and embryonic stem cellsJizhong Zou, Morgan L Maeder, Prashant Mali, et al.
Pageof 15

Showing results (81-90 of 141) with videos related to

Sort By:
Pageof 15
Elife|June 7, 2023
Combined lineage tracing and scRNA-seq reveals unexpected first heart field predominance of human iPSC differentiationFrancisco X Galdos, Carissa Lee, Soah Lee, et al.
Nucleic Acids Research|June 1, 2019
Highly efficient editing of the β-globin gene in patient-derived hematopoietic stem and progenitor cells to treat sickle cell diseaseSo Hyun Park, Ciaran M Lee, Daniel P Dever, et al.
Blood Advances|November 7, 2025
Novel humanized loss-of-function NF1 mouse model of juvenile myelomonocytic leukemiaRoshani Sinha, Rachana V Patil, Rosa Romano, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy|February 20, 2021
Correction of recessive dystrophic epidermolysis bullosa by homology-directed repair-mediated genome editingJose Bonafont, Angeles Mencía, Esteban Chacón-Solano, et al.
Nature Communications|January 3, 2024
Transient inhibition of 53BP1 increases the frequency of targeted integration in human hematopoietic stem and progenitor cellsRon Baik, M Kyle Cromer, Steve E Glenn, et al.
Nature Communications|May 15, 2015
Editing the genome to introduce a beneficial naturally occurring mutation associated with increased fetal globinBeeke Wienert, Alister P W Funnell, Laura J Norton, et al.
Molecular Therapy. Nucleic Acids|September 10, 2018
Uridine Depletion and Chemical Modification Increase Cas9 mRNA Activity and Reduce Immunogenicity without HPLC PurificationSriram Vaidyanathan, Krist T Azizian, A K M Ashiqul Haque, et al.
Biorxiv : the Preprint Server for Biology|May 20, 2024
Dual α-globin and truncated EPO receptor knockin restores hemoglobin production in α-thalassemia-derived red blood cellsSimon N Chu, Eric Soupene, Beeke Wienert, et al.
Biorxiv : the Preprint Server for Biology|March 18, 2024
Combining Cell-Intrinsic and -Extrinsic Resistance to HIV-1 By Engineering Hematopoietic Stem Cells for CCR5 Knockout and B Cell Secretion of Therapeutic AntibodiesWilliam N Feist, Sofia E Luna, Kaya Ben-Efraim, et al.
Cell Stem Cell|June 23, 2009
Gene targeting of a disease-related gene in human induced pluripotent stem and embryonic stem cellsJizhong Zou, Morgan L Maeder, Prashant Mali, et al.
Pageof 15