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Matthew Porteus

Showing results (41-50 of 45) with videos related to

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Molecular Therapy. Methods & Clinical Development|September 6, 2021
Clinically relevant gene editing in hematopoietic stem cells for the treatment of pyruvate kinase deficiencySara Fañanas-Baquero, Oscar Quintana-Bustamante, Daniel P Dever, et al.
The Journal of Experimental Medicine|September 29, 2023
Epitope-engineered human hematopoietic stem cells are shielded from CD123-targeted immunotherapyRomina Marone, Emmanuelle Landmann, Anna Devaux, et al.
Nature Medicine|July 22, 2025
Irradiation- and busulfan-free stem cell transplantation in Fanconi anemia using an anti-CD117 antibody: a phase 1b trialRajni Agarwal, Alice Bertaina, Charmaine Soco, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy|February 2, 2013
Translating the genomics revolution: the need for an international gene therapy consortium for monogenic diseasesJacques P Tremblay, Xiao Xiao, Annemieke Aartsma-Rus, et al.
JAMA|August 21, 2014
Newborn screening for severe combined immunodeficiency in 11 screening programs in the United StatesAntonia Kwan, Roshini S Abraham, Robert Currier, et al.
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Showing results (41-50 of 45) with videos related to

Sort By:
Pageof 5
You have reached the last page of results.This site can display upto 45 results.
Molecular Therapy. Methods & Clinical Development|September 6, 2021
Clinically relevant gene editing in hematopoietic stem cells for the treatment of pyruvate kinase deficiencySara Fañanas-Baquero, Oscar Quintana-Bustamante, Daniel P Dever, et al.
The Journal of Experimental Medicine|September 29, 2023
Epitope-engineered human hematopoietic stem cells are shielded from CD123-targeted immunotherapyRomina Marone, Emmanuelle Landmann, Anna Devaux, et al.
Nature Medicine|July 22, 2025
Irradiation- and busulfan-free stem cell transplantation in Fanconi anemia using an anti-CD117 antibody: a phase 1b trialRajni Agarwal, Alice Bertaina, Charmaine Soco, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy|February 2, 2013
Translating the genomics revolution: the need for an international gene therapy consortium for monogenic diseasesJacques P Tremblay, Xiao Xiao, Annemieke Aartsma-Rus, et al.
JAMA|August 21, 2014
Newborn screening for severe combined immunodeficiency in 11 screening programs in the United StatesAntonia Kwan, Roshini S Abraham, Robert Currier, et al.
Pageof 5