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Journal of Translational Medicine|September 4, 2016
A validated cellular biobank for β-thalassemiaLucia Carmela Cosenza, Laura Breda, Giulia Breveglieri, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy|March 15, 2025
CD47 peptide-cloaked lipid nanoparticles promote cell-specific mRNA deliveryTyler Ellis Papp, Jianhao Zeng, Hamna Shahnawaz, et al.
Blood|December 10, 2024
An erythroid-specific lentiviral vector improves anemia and iron metabolism in a new model of XLSACarlo Castruccio Castracani, Laura Breda, Tyler E Papp, et al.
Biomed Research International|June 23, 2015
Generation and Characterization of a Transgenic Mouse Carrying a Functional Human β -Globin Gene with the IVSI-6 Thalassemia MutationGiulia Breveglieri, Irene Mancini, Nicoletta Bianchi, et al.
Nature Medicine|March 19, 2013
Macrophages support pathological erythropoiesis in polycythemia vera and β-thalassemiaPedro Ramos, Carla Casu, Sara Gardenghi, et al.
Blood|June 13, 2025
TNFα signaling restores steady-state hematopoiesis in a TNFαKO mouse model of anemia of inflammationAmaliris Guerra, Vania Lo Presti, Ding-Wen Chen, et al.
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